Duchenne Muscular Dystrophy News and Research

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Duchenne muscular dystrophy (DMD) is a progressive muscle disorder that causes the loss of both muscle function and independence. DMD is perhaps the most prevalent of the muscular dystrophies and is the most common lethal genetic disorder diagnosed during childhood today. Each year, approximately 20,000 children worldwide are born with DMD (one of every 3,500 male children).
Early treatment with heart failure drug can improve cardiac function in young boys with DMD

Early treatment with heart failure drug can improve cardiac function in young boys with DMD

FDA approves new treatment for wide range of patients with Duchenne muscular dystrophy

FDA approves new treatment for wide range of patients with Duchenne muscular dystrophy

Researchers find striking differences between countries, age groups in access to proper care for DMD

Researchers find striking differences between countries, age groups in access to proper care for DMD

MDA celebrates FDA approval of new spinal muscular atrophy drug

MDA celebrates FDA approval of new spinal muscular atrophy drug

Cedars-Sinai receives $7.3 million grant to test safety of novel cell-based therapy in treating PAH

Cedars-Sinai receives $7.3 million grant to test safety of novel cell-based therapy in treating PAH

New drug treatment can override genetic fault that causes choroideremia

New drug treatment can override genetic fault that causes choroideremia

FDA approval of controversial drug for Duchenne muscular dystrophy raises concern and hope

FDA approval of controversial drug for Duchenne muscular dystrophy raises concern and hope

Fight for Sight, Thomas Pocklington collaborate to fund new neuro-ophthalmology research

Fight for Sight, Thomas Pocklington collaborate to fund new neuro-ophthalmology research

Immune system plays important role in Duchenne muscular dystrophy, research reveals

Immune system plays important role in Duchenne muscular dystrophy, research reveals

First comprehensive center opened in Tri-State area to mark new era in care of DMD patients

First comprehensive center opened in Tri-State area to mark new era in care of DMD patients

Department of Defense funds cardiac cell therapy trial for heart failure patients

Department of Defense funds cardiac cell therapy trial for heart failure patients

CUMC researchers uncover new details of intracellular channel that controls skeletal muscle

CUMC researchers uncover new details of intracellular channel that controls skeletal muscle

Sarepta Therapeutics wins accelerated approval from FDA for Duchenne muscular dystrophy drug

Sarepta Therapeutics wins accelerated approval from FDA for Duchenne muscular dystrophy drug

New research could pave way for safe, effective treatment for muscular dystrophy

New research could pave way for safe, effective treatment for muscular dystrophy

MDI Biological Laboratory researchers receive patent for novel heart disease drug

MDI Biological Laboratory researchers receive patent for novel heart disease drug

New gene therapeutic approach could save people suffering from muscle wasting disease

New gene therapeutic approach could save people suffering from muscle wasting disease

Key gene controls ability of adult stem cells to regenerate muscle after injury, study finds

Key gene controls ability of adult stem cells to regenerate muscle after injury, study finds

LIF-treated muscle stem cells show promise in treatment of muscular dystrophy

LIF-treated muscle stem cells show promise in treatment of muscular dystrophy

Neurofibromatosis causes benign tumor formation in normal nervous tissue

Neurofibromatosis causes benign tumor formation in normal nervous tissue

Enzyme protein neutrophil elastase may be key contributor to development of muscular dystrophy

Enzyme protein neutrophil elastase may be key contributor to development of muscular dystrophy