Hemophilia B News and Research

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Salk scientists use mRNA to successfully treat hemophilia B in mice

Salk scientists use mRNA to successfully treat hemophilia B in mice

Plant-based drug for hemophilia shows promise in animal models

Plant-based drug for hemophilia shows promise in animal models

New gene therapy for Pompe disease may replace currently available treatments

New gene therapy for Pompe disease may replace currently available treatments

AAV-based gene therapy to treat liver disorders advances into human testing

AAV-based gene therapy to treat liver disorders advances into human testing

Researchers working to develop pill for inherited bleeding disorders

Researchers working to develop pill for inherited bleeding disorders

Hemophilia B patients produce near-normal levels of clotting factor IX after gene therapy, study shows

Hemophilia B patients produce near-normal levels of clotting factor IX after gene therapy, study shows

Penn researchers use CRISPR/Cas9 gene targeting approach to treat hemophilia B in mice

Penn researchers use CRISPR/Cas9 gene targeting approach to treat hemophilia B in mice

UT Austin researchers develop new oral capsule for treating hemophilia patients

UT Austin researchers develop new oral capsule for treating hemophilia patients

ASGCT seeks to educate public and policy-makers on fundamentals of gene editing

ASGCT seeks to educate public and policy-makers on fundamentals of gene editing

New European study emphasizes need to enhance standard of haemophilia care in real life

New European study emphasizes need to enhance standard of haemophilia care in real life

Two leading non-profit organizations sign strategic affiliation to hasten drug development

Two leading non-profit organizations sign strategic affiliation to hasten drug development

New virtual reality games create better patient-experience for kids during infusions

New virtual reality games create better patient-experience for kids during infusions

Scientists link malfunctioning molecular pathways to specific heart abnormalities in SCA

Scientists link malfunctioning molecular pathways to specific heart abnormalities in SCA

UNC professor identifies research priorities to address VTE in cancer patients

UNC professor identifies research priorities to address VTE in cancer patients

TSRI awarded $20 million for first year of precision medicine initiative cohort program

TSRI awarded $20 million for first year of precision medicine initiative cohort program

Study provides more insight into treatment options for severe hemophilia A

Study provides more insight into treatment options for severe hemophilia A

Scientists use new technique to repair fibrotic liver cells within the organ

Scientists use new technique to repair fibrotic liver cells within the organ

SIPPET study may have implications for treatment of patients with severe hemophilia A

SIPPET study may have implications for treatment of patients with severe hemophilia A

Jumping genes may play crucial role in generation of cancer

Jumping genes may play crucial role in generation of cancer

European Medicines Agency approves first-ever treatment for hereditary factor X deficiency

European Medicines Agency approves first-ever treatment for hereditary factor X deficiency