Adrenoleukodystrophy News and Research

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Adrenoleukodystrophy (ALD) is one of a group of genetic disorders called the leukodystrophies that cause damage to the myelin sheath, an insulating membrane that surrounds nerve cells in the brain.
Genetix Pharmaceuticals develops a gene therapy product to treat ALD

Genetix Pharmaceuticals develops a gene therapy product to treat ALD

Gene therapy saves two children with adrenoleukodystrophy

Gene therapy saves two children with adrenoleukodystrophy

Human stem cells show promise against fatal children's diseases

Human stem cells show promise against fatal children's diseases

New approaches to genetic disease, based on cells' own ability to correct themselves

New approaches to genetic disease, based on cells' own ability to correct themselves

Study proves Lorenzo's Oil  prevents rare disease in boys

Study proves Lorenzo's Oil prevents rare disease in boys

Lorenzo's oil prevents onset of pediatric neurological disorder

Lorenzo's oil prevents onset of pediatric neurological disorder

Infants with Krabbe disease saved by cord blood stem cells

Infants with Krabbe disease saved by cord blood stem cells