Duchenne Muscular Dystrophy News and Research

RSS
Duchenne muscular dystrophy (DMD) is a progressive muscle disorder that causes the loss of both muscle function and independence. DMD is perhaps the most prevalent of the muscular dystrophies and is the most common lethal genetic disorder diagnosed during childhood today. Each year, approximately 20,000 children worldwide are born with DMD (one of every 3,500 male children).
Long-term muscle improvements shown in gene therapy study in mice

Long-term muscle improvements shown in gene therapy study in mice

Experimental drug shows promise for cystic fibrosis

Experimental drug shows promise for cystic fibrosis

Myostatin inhibitors may make injuries more likely

Myostatin inhibitors may make injuries more likely

Stem cell therapy restores muscle function in mice with muscular dystrophy

Stem cell therapy restores muscle function in mice with muscular dystrophy

Stem-cell transplantation improves muscles in MD animal model

Stem-cell transplantation improves muscles in MD animal model

Personalized medicine will alter treatment of genetic disorders

Personalized medicine will alter treatment of genetic disorders

Reprogrammed human adult stem cells rescue diseased muscle in mice

Reprogrammed human adult stem cells rescue diseased muscle in mice

Australian scientist awarded $1 million by Pfizer Australia to develop gene therapies for muscle-related diseases

Australian scientist awarded $1 million by Pfizer Australia to develop gene therapies for muscle-related diseases

Gene, stem cell therapy only needs to be 50 percent effective to create a healthy heart

Gene, stem cell therapy only needs to be 50 percent effective to create a healthy heart

Oral medication restores missing protein in boys with muscular dystrophy

Oral medication restores missing protein in boys with muscular dystrophy

Massive microRNA scan uncovers leads to treating muscle degeneration

Massive microRNA scan uncovers leads to treating muscle degeneration

Children with neuromuscular diseases at risk for decreased bone density

Children with neuromuscular diseases at risk for decreased bone density

Myoendothelial cells identified as new human source of stem cells with potential to repair muscle

Myoendothelial cells identified as new human source of stem cells with potential to repair muscle

Innovative gene therapy research for muscular dystrophy

Innovative gene therapy research for muscular dystrophy

New target for muscular dystrophy drug therapy

New target for muscular dystrophy drug therapy

Include children in research to make breakthroughs in child medicine

Include children in research to make breakthroughs in child medicine

Protein dysferlin critical for resealing heart muscle cell membranes

Protein dysferlin critical for resealing heart muscle cell membranes

New genetic test advances detection and diagnosis of muscular dystrophy

New genetic test advances detection and diagnosis of muscular dystrophy

Daily steroid treatments help boys with muscular dystrophy walk longer

Daily steroid treatments help boys with muscular dystrophy walk longer

Muscle restoration in an animal model of Duchenne muscular dystrophy

Muscle restoration in an animal model of Duchenne muscular dystrophy