Gene Therapy News and Research

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Gene therapy is an experimental technique that uses genes to treat or prevent disease. In the future, this technique may allow doctors to treat a disorder by inserting a gene into a patient’s cells instead of using drugs or surgery.
Emory scientists use new tools to detect granulins for the first time inside cells

Emory scientists use new tools to detect granulins for the first time inside cells

New version of gene editing technique corrects molecular mistakes in RNA-based diseases

New version of gene editing technique corrects molecular mistakes in RNA-based diseases

Xenotransplantation – organ transplants from animals may soon be a reality

Xenotransplantation – organ transplants from animals may soon be a reality

Clinical trial shows safety, effectiveness of pre-prepared cells to treat drug-resistant viral infections

Clinical trial shows safety, effectiveness of pre-prepared cells to treat drug-resistant viral infections

Biological bypass found safe for patients with coronary artery disease

Biological bypass found safe for patients with coronary artery disease

Nanotechnology wonders: Organ healing with a single touch!

Nanotechnology wonders: Organ healing with a single touch!

Newly discovered biomarker linked to rare metabolic disorders may facilitate better diagnosis

Newly discovered biomarker linked to rare metabolic disorders may facilitate better diagnosis

Gene-therapy administered through skin transplants could enable treatment of many diseases

Gene-therapy administered through skin transplants could enable treatment of many diseases

Study shows new method for repairing disease-causing mutation in human embryos

Study shows new method for repairing disease-causing mutation in human embryos

Bringing highly potent cell therapy products to market

Bringing highly potent cell therapy products to market

Researchers compare bone-healing effects of three low-dose growth factors

Researchers compare bone-healing effects of three low-dose growth factors

Preclinical study demonstrates efficacy of gene therapy in treatment of Duchenne muscular dystrophy

Preclinical study demonstrates efficacy of gene therapy in treatment of Duchenne muscular dystrophy

Genetic therapy for two inherited neurologic diseases moves closer to human clinical trials

Genetic therapy for two inherited neurologic diseases moves closer to human clinical trials

Developing software for cell and gene therapy supply chain tracking

Developing software for cell and gene therapy supply chain tracking

'Organic gene therapy' could be effective treatment approach for serious blood disorders

'Organic gene therapy' could be effective treatment approach for serious blood disorders

MGH researchers identify novel mechanism behind resistance to angiogenesis inhibitors

MGH researchers identify novel mechanism behind resistance to angiogenesis inhibitors

Scientists uncover new gene therapy treatment routes for motor neurone disease

Scientists uncover new gene therapy treatment routes for motor neurone disease

FDA panel recommends new breakthrough gene therapy for B-cell acute lymphoblastic leukemia (ALL)

FDA panel recommends new breakthrough gene therapy for B-cell acute lymphoblastic leukemia (ALL)

FDA advisory committee recommends Novartis' CAR-T therapy for young leukemia patients

FDA advisory committee recommends Novartis' CAR-T therapy for young leukemia patients

New partnership to advance novel airway-delivered gene therapy for treating pulmonary hypertension

New partnership to advance novel airway-delivered gene therapy for treating pulmonary hypertension