Gene Therapy News and Research

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Gene therapy is an experimental technique that uses genes to treat or prevent disease. In the future, this technique may allow doctors to treat a disorder by inserting a gene into a patient’s cells instead of using drugs or surgery.
Researchers identify novel cellular entry factor for AAV vector types

Researchers identify novel cellular entry factor for AAV vector types

Synthego adopts GMP standards for producing sgRNA

Synthego adopts GMP standards for producing sgRNA

Researchers identify potential way to halt age-related macular degeneration

Researchers identify potential way to halt age-related macular degeneration

Potential Parkinson's treatment effectively targets a specific group of brain cells

Potential Parkinson's treatment effectively targets a specific group of brain cells

Study shows how gene therapy may help protect against vision loss in multiple sclerosis

Study shows how gene therapy may help protect against vision loss in multiple sclerosis

Discovery of new killer T-cell offers hope of a 'one-size-fits-all' cancer therapy

Discovery of new killer T-cell offers hope of a 'one-size-fits-all' cancer therapy

SITESEEKER to be used for Otsuka’s therapeutics discovery programs

SITESEEKER to be used for Otsuka’s therapeutics discovery programs

Horizon Discovery to offer novel base editing technology for clinical research

Horizon Discovery to offer novel base editing technology for clinical research

Scientists discover a new way to combine coding languages into single "bilingual" molecule

Scientists discover a new way to combine coding languages into single "bilingual" molecule

Scientists find way to combine two main coding languages into single 'bilingual' molecule

Scientists find way to combine two main coding languages into single 'bilingual' molecule

Single-particle method helps determine isoelectric point of viruses

Single-particle method helps determine isoelectric point of viruses

Researchers report first structural model for key enzyme associated with inherited eye diseases

Researchers report first structural model for key enzyme associated with inherited eye diseases

Biodegradable nanoparticle can deliver 'suicide gene' to pediatric brain tumor cells in mice

Biodegradable nanoparticle can deliver 'suicide gene' to pediatric brain tumor cells in mice

Dog study suggests that AAV in gene therapy could induce cancer

Dog study suggests that AAV in gene therapy could induce cancer

Mayo Clinic researchers seek radical new approach to treat cocaine addition

Mayo Clinic researchers seek radical new approach to treat cocaine addition

Using CRISPR to switch off pain gene becomes a possibility with new study

Using CRISPR to switch off pain gene becomes a possibility with new study

Study shows safety, long-term beneficial impact of gene therapy for patients with Hemophilia A

Study shows safety, long-term beneficial impact of gene therapy for patients with Hemophilia A

Study shows the feasibility of using gene therapy to treat chronic traumatic encephalopathy

Study shows the feasibility of using gene therapy to treat chronic traumatic encephalopathy

IU researchers identify potential target to improve functional recovery after spinal cord injury

IU researchers identify potential target to improve functional recovery after spinal cord injury

Study uncovers a previously unknown subtype of muscle stem cells

Study uncovers a previously unknown subtype of muscle stem cells