Hemophilia A News and Research

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LogicBio team to present data on preclinical effectiveness of GeneRide platform

LogicBio team to present data on preclinical effectiveness of GeneRide platform

Breakthrough study promises to bring gene-editing technology much closer to therapeutic reality

Breakthrough study promises to bring gene-editing technology much closer to therapeutic reality

UCLA-developed nanospears could make gene therapies safer, faster and more cost-effective

UCLA-developed nanospears could make gene therapies safer, faster and more cost-effective

Of ‘miracles’ and money: Why hemophilia drugs are so expensive

Of ‘miracles’ and money: Why hemophilia drugs are so expensive

Study unravels novel cellular and molecular pathway that regulates innate, adaptive immunity

Study unravels novel cellular and molecular pathway that regulates innate, adaptive immunity

Scientists discover adult endothelial stem cells capable of generating fully functional blood vessels

Scientists discover adult endothelial stem cells capable of generating fully functional blood vessels

Biomedical engineers develop miniature self-sealing wound model

Biomedical engineers develop miniature self-sealing wound model

Sangamo and Pfizer partner for development of new zinc finger protein gene therapy to treat ALS

Sangamo and Pfizer partner for development of new zinc finger protein gene therapy to treat ALS

Strategies to prevent and treat acute chest syndrome in children with sickle cell disease

Strategies to prevent and treat acute chest syndrome in children with sickle cell disease

Groundbreaking gene therapy trial brings cure for hemophilia closer

Groundbreaking gene therapy trial brings cure for hemophilia closer

New, more easily administered therapies offer benefits for bleeding and clotting disorders

New, more easily administered therapies offer benefits for bleeding and clotting disorders

Gene therapy shows promising effect against blood clots, study states

Gene therapy shows promising effect against blood clots, study states

NIH grant supports research on cellular mechanisms governing longevity

NIH grant supports research on cellular mechanisms governing longevity

FDA approves new drug to treat bleeding in hemophilia A patients

FDA approves new drug to treat bleeding in hemophilia A patients

FDA permits marketing of first electric stimulation device to reduce opioid withdrawal symptoms

FDA permits marketing of first electric stimulation device to reduce opioid withdrawal symptoms

New category of immunotherapy appears safe to use in patients with both cancer and HIV

New category of immunotherapy appears safe to use in patients with both cancer and HIV

FDA advisory committee vote 16-0 for first even gene therapy for rare blindness

FDA advisory committee vote 16-0 for first even gene therapy for rare blindness

New microcapsules represent promising vectors for application of genome-editing tools

New microcapsules represent promising vectors for application of genome-editing tools

Pfizer announces launch two new digital innovations to help people living with hemophilia

Pfizer announces launch two new digital innovations to help people living with hemophilia

Shire partners with MicroHealth to support secure care monitoring tool for hemophilia patients with inhibitors

Shire partners with MicroHealth to support secure care monitoring tool for hemophilia patients with inhibitors