Hemophilia B News and Research

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International team to set how gene therapies in hemophilia should be measured for effectiveness

International team to set how gene therapies in hemophilia should be measured for effectiveness

Altered virus could help more patients to become eligible for human gene therapy trials

Altered virus could help more patients to become eligible for human gene therapy trials

Scripps scientists make important advance in HIV vaccine design

Scripps scientists make important advance in HIV vaccine design

Sangamo Therapeutics and Pfizer team up for development of Hemophilia A gene therapy

Sangamo Therapeutics and Pfizer team up for development of Hemophilia A gene therapy

Novo Nordisk introduces new web-based portal that helps patients track their hemophilia treatment

Novo Nordisk introduces new web-based portal that helps patients track their hemophilia treatment

UMass Amherst study highlights unmet drug needs of patients with rare diseases

UMass Amherst study highlights unmet drug needs of patients with rare diseases

Salk scientists use mRNA to successfully treat hemophilia B in mice

Salk scientists use mRNA to successfully treat hemophilia B in mice

Plant-based drug for hemophilia shows promise in animal models

Plant-based drug for hemophilia shows promise in animal models

New gene therapy for Pompe disease may replace currently available treatments

New gene therapy for Pompe disease may replace currently available treatments

AAV-based gene therapy to treat liver disorders advances into human testing

AAV-based gene therapy to treat liver disorders advances into human testing

Researchers working to develop pill for inherited bleeding disorders

Researchers working to develop pill for inherited bleeding disorders

Hemophilia B patients produce near-normal levels of clotting factor IX after gene therapy, study shows

Hemophilia B patients produce near-normal levels of clotting factor IX after gene therapy, study shows

Penn researchers use CRISPR/Cas9 gene targeting approach to treat hemophilia B in mice

Penn researchers use CRISPR/Cas9 gene targeting approach to treat hemophilia B in mice

UT Austin researchers develop new oral capsule for treating hemophilia patients

UT Austin researchers develop new oral capsule for treating hemophilia patients

ASGCT seeks to educate public and policy-makers on fundamentals of gene editing

ASGCT seeks to educate public and policy-makers on fundamentals of gene editing

New European study emphasizes need to enhance standard of haemophilia care in real life

New European study emphasizes need to enhance standard of haemophilia care in real life

Two leading non-profit organizations sign strategic affiliation to hasten drug development

Two leading non-profit organizations sign strategic affiliation to hasten drug development

New virtual reality games create better patient-experience for kids during infusions

New virtual reality games create better patient-experience for kids during infusions

Scientists link malfunctioning molecular pathways to specific heart abnormalities in SCA

Scientists link malfunctioning molecular pathways to specific heart abnormalities in SCA

UNC professor identifies research priorities to address VTE in cancer patients

UNC professor identifies research priorities to address VTE in cancer patients