Muscular Atrophy News and Research

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Study finds attractive therapeutic target for treatment of Kennedy's disease and prostrate cancer

Study finds attractive therapeutic target for treatment of Kennedy's disease and prostrate cancer

Statement related to data inaccuracies with newly approved gene therapy

Statement related to data inaccuracies with newly approved gene therapy

New vaccine shows promise against toughest HIV strains

New vaccine shows promise against toughest HIV strains

BIA Separations selected to support AveXis’ gene therapy pipeline

BIA Separations selected to support AveXis’ gene therapy pipeline

Newly approved gene therapy for SMA is based on delivery vehicle discovered by Penn expert

Newly approved gene therapy for SMA is based on delivery vehicle discovered by Penn expert

$150,000 grant will support research on spinal muscular atrophy

$150,000 grant will support research on spinal muscular atrophy

Unique gene therapy approach paves new way to tackle rare, inherited diseases

Unique gene therapy approach paves new way to tackle rare, inherited diseases

New form of therapy may stop or reverse progressive vision loss

New form of therapy may stop or reverse progressive vision loss

Biogen and Eisai present detailed results from phase 1b study of aducanumab at CTAD meeting

Biogen and Eisai present detailed results from phase 1b study of aducanumab at CTAD meeting

Novartis: Lancet publishes pioneering study of Aimovig’s efficacy in episodic migraine patients

Novartis: Lancet publishes pioneering study of Aimovig’s efficacy in episodic migraine patients

Genentech announces clinical data from studies investigating risdiplam in spinal muscular atrophy

Genentech announces clinical data from studies investigating risdiplam in spinal muscular atrophy

Researchers discover how nerve cells control movement

Researchers discover how nerve cells control movement

Urine exRNA may be source of biomarkers for muscular dystrophy

Urine exRNA may be source of biomarkers for muscular dystrophy

Biogen and Eisai announce results of LTE Phase 1b study of aducanumab for treating MCI

Biogen and Eisai announce results of LTE Phase 1b study of aducanumab for treating MCI

Study links spinal muscular atrophy disease expression with haplotypes

Study links spinal muscular atrophy disease expression with haplotypes

SMA treatment may be effective even if started in children seven months and older

SMA treatment may be effective even if started in children seven months and older

Alternative method identified for delivering nusinersen to spinal muscular atrophy patients

Alternative method identified for delivering nusinersen to spinal muscular atrophy patients

MDA announces 34 new grants totaling $9.9 million to accelerate neuromuscular research

MDA announces 34 new grants totaling $9.9 million to accelerate neuromuscular research

Study findings highlight importance of early detection of SMA through newborn screening

Study findings highlight importance of early detection of SMA through newborn screening

Novel therapeutic approach alleviates ALS-related muscular atrophy in mouse models

Novel therapeutic approach alleviates ALS-related muscular atrophy in mouse models