Muscular Dystrophy News and Research

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The muscular dystrophies (MD) are a group of more than 30 genetic diseases characterized by progressive weakness and degeneration of the skeletal muscles that control movement. Some forms of MD are seen in infancy or childhood, while others may not appear until middle age or later. The disorders differ in terms of the distribution and extent of muscle weakness (some forms of MD also affect cardiac muscle), age of onset, rate of progression, and pattern of inheritance.
Scientists create artificial human muscles

Scientists create artificial human muscles

FDA chief says he’s open to rethinking incentives on orphan drugs

FDA chief says he’s open to rethinking incentives on orphan drugs

UCLA researchers reveal reversibility of Friedreich's ataxia in mouse models

UCLA researchers reveal reversibility of Friedreich's ataxia in mouse models

Study reveals biology behind why muscle stem cells respond differently to aging or injury

Study reveals biology behind why muscle stem cells respond differently to aging or injury

Researchers discover how high glucose levels in pregnancy affect baby's heart

Researchers discover how high glucose levels in pregnancy affect baby's heart

Researchers reveal pathological mechanisms in congenital myotonic dystrophy

Researchers reveal pathological mechanisms in congenital myotonic dystrophy

SLU scientists provide promising approach in designing new drugs for DMD

SLU scientists provide promising approach in designing new drugs for DMD

UT Southwestern researchers develop improved gene-editing technique to correct DMD mutations

UT Southwestern researchers develop improved gene-editing technique to correct DMD mutations

New initiative aims to improve chances of medicines receiving positive HTA decisions

New initiative aims to improve chances of medicines receiving positive HTA decisions

New research shows how a gene can fuel obesity in mice

New research shows how a gene can fuel obesity in mice

Clinical trial results could lead to treatment of heart disease in Duchenne muscular dystrophy patients

Clinical trial results could lead to treatment of heart disease in Duchenne muscular dystrophy patients

MDA announces 13 new research grants to advance treatment for neuromuscular diseases

MDA announces 13 new research grants to advance treatment for neuromuscular diseases

SLU researcher reports success in identifying new drug targets for muscular dystrophy

SLU researcher reports success in identifying new drug targets for muscular dystrophy

Study identifies predictors of poor outcomes in Duchenne muscular dystrophy patients

Study identifies predictors of poor outcomes in Duchenne muscular dystrophy patients

Specific regions of silenced DNA help define cell's identity, study suggests

Specific regions of silenced DNA help define cell's identity, study suggests

CRISPR-Gold corrects gene mutations in mice with Duchenne muscular dystrophy

CRISPR-Gold corrects gene mutations in mice with Duchenne muscular dystrophy

Novel gene therapy can inhibit, reverse multiple sclerosis in mouse models

Novel gene therapy can inhibit, reverse multiple sclerosis in mouse models

University Of Minnesota scientists describe breakthrough in research related to FSHD

University Of Minnesota scientists describe breakthrough in research related to FSHD

Penn researchers find abnormally shortened telomeres in young DMD patients’ muscle stem cells

Penn researchers find abnormally shortened telomeres in young DMD patients’ muscle stem cells

Potential rare gene mutation could act as predictor for schizophrenia and autism

Potential rare gene mutation could act as predictor for schizophrenia and autism