Muscular Dystrophy News and Research

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The muscular dystrophies (MD) are a group of more than 30 genetic diseases characterized by progressive weakness and degeneration of the skeletal muscles that control movement. Some forms of MD are seen in infancy or childhood, while others may not appear until middle age or later. The disorders differ in terms of the distribution and extent of muscle weakness (some forms of MD also affect cardiac muscle), age of onset, rate of progression, and pattern of inheritance.
Study uncovers gene that hides tumor cells from immunotherapy

Study uncovers gene that hides tumor cells from immunotherapy

Nanoparticles used to deliver CRISPR gene editing tools into the cell

Nanoparticles used to deliver CRISPR gene editing tools into the cell

New drug provides hope for patients with Duchenne muscular dystrophy

New drug provides hope for patients with Duchenne muscular dystrophy

Study uncovers potential modifier genes in patients with Charcot-Marie-Tooth disease

Study uncovers potential modifier genes in patients with Charcot-Marie-Tooth disease

New discovery could improve therapies for Duchenne muscular dystrophy

New discovery could improve therapies for Duchenne muscular dystrophy

Study raises the prospect of new therapies to delay muscle atrophy

Study raises the prospect of new therapies to delay muscle atrophy

Scientists successfully carry out gene editing in vivo

Scientists successfully carry out gene editing in vivo

Lithium improves muscle size and strength in mice with limb girdle muscular dystrophy

Lithium improves muscle size and strength in mice with limb girdle muscular dystrophy

Study clarifies how 3D organization of genome is regulated at onset of skeletal muscle formation

Study clarifies how 3D organization of genome is regulated at onset of skeletal muscle formation

Newly discovered molecules safely halt the gene editing process

Newly discovered molecules safely halt the gene editing process

Study discovers origin of neurofibromas that develop throughout the skin of NF1 patients

Study discovers origin of neurofibromas that develop throughout the skin of NF1 patients

MDI Biological Laboratory receives $30,000 to support course in organoid technology

MDI Biological Laboratory receives $30,000 to support course in organoid technology

Discovery of small-molecule inhibitors could enable precise control over CRISPR-Cas9 genome editing

Discovery of small-molecule inhibitors could enable precise control over CRISPR-Cas9 genome editing

Reviving the heart's regenerative capacities using microRNAs

Reviving the heart's regenerative capacities using microRNAs

Research uncovers critical RNA processing aberrations in ALS and FTD

Research uncovers critical RNA processing aberrations in ALS and FTD

Scientists investigate processes that lead to neuronal death in ALS patients

Scientists investigate processes that lead to neuronal death in ALS patients

Novo Biosciences achieves major milestones in its new drug to treat heart disease and DMD

Novo Biosciences achieves major milestones in its new drug to treat heart disease and DMD

New strategy for editing and repairing genetic mutation associated with microduplications

New strategy for editing and repairing genetic mutation associated with microduplications

Bringing Maine researchers together to identify solutions to opioid epidemic in Maine

Bringing Maine researchers together to identify solutions to opioid epidemic in Maine

First-of-its-kind human trial of new brain reading device to help speech and movement

First-of-its-kind human trial of new brain reading device to help speech and movement