Prader Willi Syndrome News and Research

RSS
IBR receives $1.95 million NIH grant for research on rare diseases

IBR receives $1.95 million NIH grant for research on rare diseases

PWSA (USA) announces support for H.R.4144 - Ending the Diagnostic Odyssey Act of 2019

PWSA (USA) announces support for H.R.4144 - Ending the Diagnostic Odyssey Act of 2019

New approach to waking up sleeping genes could help people with Prader-Willi syndrome

New approach to waking up sleeping genes could help people with Prader-Willi syndrome

ausEE promotes Australia’s Feeding Tube Awareness Week

ausEE promotes Australia’s Feeding Tube Awareness Week

Ferring announces FDA approval of ZOMACTON for injection in four new pediatric indications

Ferring announces FDA approval of ZOMACTON for injection in four new pediatric indications

Discovery may offer new therapeutic approach for kids with Prader-Willi syndrome

Discovery may offer new therapeutic approach for kids with Prader-Willi syndrome

Potential drug could become first effective treatment option for Prader-Willi syndrome

Potential drug could become first effective treatment option for Prader-Willi syndrome

Experimental drug improves survival, growth outcomes in mouse model of Prader-Willi syndrome

Experimental drug improves survival, growth outcomes in mouse model of Prader-Willi syndrome

CHLA study provides novel insights into the brain mechanisms linked to Prader-Willi syndrome

CHLA study provides novel insights into the brain mechanisms linked to Prader-Willi syndrome

Scientists discover unexpected functions of snoRNAs that explains cause of some diseases

Scientists discover unexpected functions of snoRNAs that explains cause of some diseases

New UCL study highlights genes associated with schizophrenia and obesity

New UCL study highlights genes associated with schizophrenia and obesity

FDA awards research grants to boost product development for patients with rare diseases

FDA awards research grants to boost product development for patients with rare diseases

Bariatric surgery results in substantial weight loss in overweight children with Prader-Willi syndrome

Bariatric surgery results in substantial weight loss in overweight children with Prader-Willi syndrome

Rhythm Metabolic awarded FDA grant to advance ongoing setmelanotide clinical trial in Prader-Willi syndrome

Rhythm Metabolic awarded FDA grant to advance ongoing setmelanotide clinical trial in Prader-Willi syndrome

Rhythm Metabolic completes $40 million Series A financing

Rhythm Metabolic completes $40 million Series A financing

Rhythm announces initiation of two setmelanotide Phase 2 trials for treatment of PWS, POMC-null obesity

Rhythm announces initiation of two setmelanotide Phase 2 trials for treatment of PWS, POMC-null obesity

Alizé Pharma presents clinical results from the AZP-531 program at the ADA 75th Scientific Sessions

Alizé Pharma presents clinical results from the AZP-531 program at the ADA 75th Scientific Sessions

Johns Hopkins researchers link sperm with specific 'epigenetic tags' to autism

Johns Hopkins researchers link sperm with specific 'epigenetic tags' to autism

Rhythm, Actavis announce initiation of relamorelin Phase 2b trial for treatment of diabetic gastroparesis

Rhythm, Actavis announce initiation of relamorelin Phase 2b trial for treatment of diabetic gastroparesis

Alizé Pharma announces launch of AZP-531 Phase II trial in patients with Prader-Willi syndrome

Alizé Pharma announces launch of AZP-531 Phase II trial in patients with Prader-Willi syndrome