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Creative solutions to enhance patient's point of view in neuromuscular research

Creative solutions to enhance patient's point of view in neuromuscular research

Researchers describe first case of patient affected by dysfunctions in SLC28 gene family

Researchers describe first case of patient affected by dysfunctions in SLC28 gene family

NIH grants awarded to Nanoscope to recruit talent and develop optogenetic delivery platforms

NIH grants awarded to Nanoscope to recruit talent and develop optogenetic delivery platforms

Women with IBD have increased risk of developing mental illness, finds study

Women with IBD have increased risk of developing mental illness, finds study

FDA approves new treatment for rare disease of the bone marrow and blood

FDA approves new treatment for rare disease of the bone marrow and blood

WU biomedical engineer makes a significant step toward precision medicine

WU biomedical engineer makes a significant step toward precision medicine

Sickest children could benefit from split liver transplants

Sickest children could benefit from split liver transplants

Scientists create patient-specific model to identify most effective treatment for appendix cancer

Scientists create patient-specific model to identify most effective treatment for appendix cancer

TGen receives PayPal grant to underwrite costs of genetic tests for children with rare disorders

TGen receives PayPal grant to underwrite costs of genetic tests for children with rare disorders

CTF along with NTAP and Sage announce first-ever open data portal for neurofibromatosis

CTF along with NTAP and Sage announce first-ever open data portal for neurofibromatosis

Study provides new understanding of mysterious 'hereditary swelling'

Study provides new understanding of mysterious 'hereditary swelling'

A Preclinical Solution to Studying Neurological Diseases

A Preclinical Solution to Studying Neurological Diseases

Insilico Medicine to introduce 'Cure a disease in a year' program at Biodata World Congress 2018

Insilico Medicine to introduce 'Cure a disease in a year' program at Biodata World Congress 2018

Treating children with 'bubble baby disease'

Treating children with 'bubble baby disease'

Researchers create new accessible staging system to predict survival for patients with AL amyloidosis

Researchers create new accessible staging system to predict survival for patients with AL amyloidosis

Geneticists decipher new gene responsible for rare form of hair loss

Geneticists decipher new gene responsible for rare form of hair loss

New form of therapy may stop or reverse progressive vision loss

New form of therapy may stop or reverse progressive vision loss

Goethe University plays important role in rare disease research

Goethe University plays important role in rare disease research

FOTIVDA expected to be included in new ESMO guidelines for advanced renal cell carcinoma

FOTIVDA expected to be included in new ESMO guidelines for advanced renal cell carcinoma

X4 Pharmaceuticals announces clinical data of X4P-001-IO and Opdivo in patients with clear cell renal cell carcinoma

X4 Pharmaceuticals announces clinical data of X4P-001-IO and Opdivo in patients with clear cell renal cell carcinoma