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A Preclinical Solution to Studying Neurological Diseases

A Preclinical Solution to Studying Neurological Diseases

Insilico Medicine to introduce 'Cure a disease in a year' program at Biodata World Congress 2018

Insilico Medicine to introduce 'Cure a disease in a year' program at Biodata World Congress 2018

Treating children with 'bubble baby disease'

Treating children with 'bubble baby disease'

Researchers create new accessible staging system to predict survival for patients with AL amyloidosis

Researchers create new accessible staging system to predict survival for patients with AL amyloidosis

Geneticists decipher new gene responsible for rare form of hair loss

Geneticists decipher new gene responsible for rare form of hair loss

New form of therapy may stop or reverse progressive vision loss

New form of therapy may stop or reverse progressive vision loss

Goethe University plays important role in rare disease research

Goethe University plays important role in rare disease research

FOTIVDA expected to be included in new ESMO guidelines for advanced renal cell carcinoma

FOTIVDA expected to be included in new ESMO guidelines for advanced renal cell carcinoma

X4 Pharmaceuticals announces clinical data of X4P-001-IO and Opdivo in patients with clear cell renal cell carcinoma

X4 Pharmaceuticals announces clinical data of X4P-001-IO and Opdivo in patients with clear cell renal cell carcinoma

Leadiant Biosciences announces FDA approval of Revcovi for treating pediatric, adult ADA-SCID patients

Leadiant Biosciences announces FDA approval of Revcovi for treating pediatric, adult ADA-SCID patients

Alnylam announces positive results from Phase 1/2 study of lumasiran for treating primary hyperoxaluria-1

Alnylam announces positive results from Phase 1/2 study of lumasiran for treating primary hyperoxaluria-1

Alnylam submits CTA application to MHRA to initiate Phase 1/2 study of ALN-AAT02

Alnylam submits CTA application to MHRA to initiate Phase 1/2 study of ALN-AAT02

New project identifies immune checkpoint inhibition as potential treatment for angiosarcomas

New project identifies immune checkpoint inhibition as potential treatment for angiosarcomas

Lumos acquires license for LUM-201 drug that promotes secretion of growth hormone

Lumos acquires license for LUM-201 drug that promotes secretion of growth hormone

Alexion announces positive results from Phase 3 PREVENT study of Soliris in patients with NMOSD

Alexion announces positive results from Phase 3 PREVENT study of Soliris in patients with NMOSD

Salk research in yeast leads to serendipitous finding about hypomyelinating leukodystrophy

Salk research in yeast leads to serendipitous finding about hypomyelinating leukodystrophy

Investigators identify group of blood metabolites that could help detect autism

Investigators identify group of blood metabolites that could help detect autism

BeiGene collaborates with SpringWorks to evaluate new combinational therapy for solid tumors

BeiGene collaborates with SpringWorks to evaluate new combinational therapy for solid tumors

Pfizer terminates clinical studies evaluating domagrozumab for treatment of Duchenne muscular dystrophy

Pfizer terminates clinical studies evaluating domagrozumab for treatment of Duchenne muscular dystrophy

Eagle Pharmaceuticals completes enrollment of second clinical study to evaluate safety, efficacy of RYANODEX

Eagle Pharmaceuticals completes enrollment of second clinical study to evaluate safety, efficacy of RYANODEX