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UM launches CAR-T clinical trial for patients with myasthenia gravis

UM launches CAR-T clinical trial for patients with myasthenia gravis

FDA keeps brand-name drugs on a fast path to market ― despite manufacturing concerns

FDA keeps brand-name drugs on a fast path to market ― despite manufacturing concerns

Molecular gatekeepers that regulate calcium ions vital for muscle health and repair

Molecular gatekeepers that regulate calcium ions vital for muscle health and repair

Discovery in monkeys could pave way for treatment of Bardet-Biedl Syndrome

Discovery in monkeys could pave way for treatment of Bardet-Biedl Syndrome

Breakthrough study suggests ways to develop treatments for rare genetic skin disease

Breakthrough study suggests ways to develop treatments for rare genetic skin disease

$5 million in federal funding to accelerate potential treatments for urea cycle disorders

$5 million in federal funding to accelerate potential treatments for urea cycle disorders

Study: More than 300 million people affected worldwide by rare diseases

Study: More than 300 million people affected worldwide by rare diseases

Hong Kong Baptist University receives FDA orphan drug designation for novel aptamer

Hong Kong Baptist University receives FDA orphan drug designation for novel aptamer

LSU Health New Orleans awarded $1.74 million to advance research on Usher syndrome

LSU Health New Orleans awarded $1.74 million to advance research on Usher syndrome

Cytel hosts Complex Innovative Trial Design Symposium and East Training in Boston

Cytel hosts Complex Innovative Trial Design Symposium and East Training in Boston

Study suggests new model of treatment for heart attack or stroke victims

Study suggests new model of treatment for heart attack or stroke victims

How Is Ophthalmology Changing To Meet New Challenges?

How Is Ophthalmology Changing To Meet New Challenges?

Cleveland Clinic-led researchers develop novel genetic-based epilepsy risk scores

Cleveland Clinic-led researchers develop novel genetic-based epilepsy risk scores

Cincinnati Children's receives NIH grant renewal for collaborative research into eosinophilic disorders

Cincinnati Children's receives NIH grant renewal for collaborative research into eosinophilic disorders

GW researchers to study the underlying pathophysiology of myasthenia gravis

GW researchers to study the underlying pathophysiology of myasthenia gravis

NIH grants boost rare diseases research efforts

NIH grants boost rare diseases research efforts

$28 million grant supports Cincinnati Children's role as coordinating center for Rare Diseases Clinical Research Network

$28 million grant supports Cincinnati Children's role as coordinating center for Rare Diseases Clinical Research Network

Medical professional offers unique perspective as father of a child with rare movement disorder

Medical professional offers unique perspective as father of a child with rare movement disorder

Research reveals new mechanism which could lead to premature aging in mother cells

Research reveals new mechanism which could lead to premature aging in mother cells

Chan Zuckerberg Initiative supports a patient-led movement to cure ALS

Chan Zuckerberg Initiative supports a patient-led movement to cure ALS