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   Advances in Gene Silencing and Editing for Rare DisordersAdvances in Gene Silencing and Editing for Rare Disorders
 
Significant progress in Huntington's disease treatment: AMT-130 therapy achieves 75% slowing of disease progression using innovative gene silencing techniques.
 
   Gene therapy shows long-term success in children with rare immune disorderGene therapy shows long-term success in children with rare immune disorder
 
Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the long-term safety and efficacy of the curative treatment, in a study led by a UCL researcher.
 
 Combating Influenza A Virus with CRISPR and Human Lung Organ Chips
 
Combating Influenza A Virus with CRISPR and Human Lung Organ ChipsThe Influenza A virus (IAV) has been the cause of six major flu pandemics, responsible for 50 to 100 million deaths globally.
 
 
 New Elastic Calcium Phosphate Material Mimics Bone Structure
 
New Elastic Calcium Phosphate Material Mimics Bone StructureThe elastic calcium phosphate material developed by HKUMed enhances orthopedic surgery outcomes, offering superior biocompatibility and mechanical properties.
 
 
 Experimental gene therapy restores immune system function in children with genetic immune disorder
 
Experimental gene therapy restores immune system function in children with genetic immune disorderAn experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has restored and maintained immune system function in 59 of 62 children born with ADA-SCID, a rare and deadly genetic immune disorder.
 
 
 How Plants are Being Engineered to Thrive Under Climate Extremes
 
How Plants are Being Engineered to Thrive Under Climate ExtremesInnovative genetic engineering strategies are transforming crops, enabling them to withstand extreme climate conditions and support food security.
 
 
 Smart Proteins Bring Precision Drug Delivery Closer to Reality
 
Smart Proteins Bring Precision Drug Delivery Closer to RealityTargeted drug delivery is a powerful and promising area of medicine. Therapies that pinpoint the exact areas of the body where they're needed - and nowhere they're not - can reduce the medicine dosage and avoid potentially harmful "off target" effects elsewhere in the body.
 
 
 GlyTR Therapeutics Unveils Groundbreaking Glycan-Targeting Cancer Immunotherapy
 
GlyTR Therapeutics Unveils Groundbreaking Glycan-Targeting Cancer ImmunotherapyGlyTR Therapeutics, a biotech company pioneering development of glycan-targeting cancer immunotherapies, announced the publication of its foundational technology in the journal, Cell.
 
 
 Study Uncovers Hundreds of New Viruses Living Inside the Gut Bacteria
 
Study Uncovers Hundreds of New Viruses Living Inside the Gut BacteriaHundreds of new viruses living inside bacteria within our gut have been discovered in an international study led by Professor Jeremy J. Barr from Monash University's School of Biological Sciences and Associate Professor Sam Forster from Hudson Institute of Medical Research.
 
 

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