Hemophilia News and Research

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Hemophilia is a rare, inherited bleeding disorder in which your blood doesn’t clot normally. If you have hemophilia, you may bleed for a longer time than others after an injury. You also may bleed internally, especially in your knees, ankles, and elbows. This bleeding can damage your organs or tissues and, sometimes, be fatal.
UMass Amherst study highlights unmet drug needs of patients with rare diseases

UMass Amherst study highlights unmet drug needs of patients with rare diseases

Salk scientists use mRNA to successfully treat hemophilia B in mice

Salk scientists use mRNA to successfully treat hemophilia B in mice

TSRI scientists describe how key molecules in the brain work together to trigger intense anxiety

TSRI scientists describe how key molecules in the brain work together to trigger intense anxiety

Plant-based drug for hemophilia shows promise in animal models

Plant-based drug for hemophilia shows promise in animal models

TSRI chemists create new technique for constructing chiral drug molecules

TSRI chemists create new technique for constructing chiral drug molecules

Deep brain stimulation can reduce heroin relapse in rat models of addiction, TSRI study shows

Deep brain stimulation can reduce heroin relapse in rat models of addiction, TSRI study shows

TSRI study offers first look at early stages of brain development in patients with Fragile X syndrome

TSRI study offers first look at early stages of brain development in patients with Fragile X syndrome

New gene therapy for Pompe disease may replace currently available treatments

New gene therapy for Pompe disease may replace currently available treatments

TSRI biologists uncover new mechanism behind sense of touch

TSRI biologists uncover new mechanism behind sense of touch

TSRI scientists develop new tool to uncover molecular details of protein structure

TSRI scientists develop new tool to uncover molecular details of protein structure

New TSRI study sheds light on how the brain stores memories

New TSRI study sheds light on how the brain stores memories

AAV-based gene therapy to treat liver disorders advances into human testing

AAV-based gene therapy to treat liver disorders advances into human testing

TSRI scientists develop new approach for understanding diverse effects of endocrine-disruptors

TSRI scientists develop new approach for understanding diverse effects of endocrine-disruptors

A new strategy to fight prostate cancer

A new strategy to fight prostate cancer

Researchers working to develop pill for inherited bleeding disorders

Researchers working to develop pill for inherited bleeding disorders

TSRI scientists shed light on how antiviral drug stops influenza infections

TSRI scientists shed light on how antiviral drug stops influenza infections

TSRI scientist receives Outstanding Investigator Grant to focus on memory formation research

TSRI scientist receives Outstanding Investigator Grant to focus on memory formation research

Hemophilia B patients produce near-normal levels of clotting factor IX after gene therapy, study shows

Hemophilia B patients produce near-normal levels of clotting factor IX after gene therapy, study shows

Penn researchers use CRISPR/Cas9 gene targeting approach to treat hemophilia B in mice

Penn researchers use CRISPR/Cas9 gene targeting approach to treat hemophilia B in mice

UT Austin researchers develop new oral capsule for treating hemophilia patients

UT Austin researchers develop new oral capsule for treating hemophilia patients