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Early diagnosis and treatment is crucial for pulmonary hypertension, a rare but deadly disease

19. November 2009 06:56
We often hear about the perils of high blood pressure, but many Canadians are unaware that high blood pressure in the lungs - known as pulmonary hypertension (PH) - can also have fatal consequences. This month, the Pulmonary Hypertension Association of Canada hopes to raise awareness about PH - a rare but serious disease that can strike at any time and has no regard for race, age or gender. [More]

Myeloma UK launches innovative clinical trial network

16. November 2009 08:29
Yorkshire myeloma patients are set to be among the first to benefit from an innovative Myeloma Clinical Trial Network launched by Myeloma UK. [More]

NMO patients are misdiagnosed with Multiple Sclerosis, says Mayo Clinic neurologist

12. November 2009 03:18
Thousands of Neuromyelitis Optica (NMO) patients are potentially being misdiagnosed with Multiple Sclerosis (MS), according to Mayo Clinic Neurologist Sean Pittock, M.D., largely due to lack of awareness of NMO within the medical community. [More]

In-depth information of the American, European and Japanese pharmaceutical markets

11. November 2009 05:55
Reportlinker.com announces that a new market research report is available in its catalogue: Pharmaceutical Pricing, Reimbursement and Parallel Trade 2006 [More]

PPMD awards $75,000 grant to University of California professor for Duchenne muscular dystrophy research

6. November 2009 23:48
Patricia A. Furlong, Founding President and CEO of Parent Project Muscular Dystrophy (PPMD), the largest non-profit organization in the United States focused on finding a cure for Duchenne muscular dystrophy (Duchenne), announced today the latest recipient of the End Duchenne Grant Award Program. [More]

Posted in: Medical Condition News

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FDA grants orphan drug designation for Sunesis Pharmaceuticals' voreloxin

6. November 2009 01:56
Sunesis Pharmaceuticals, Inc. today announced that the U.S. Food and Drug Administration has granted voreloxin orphan drug designation for the treatment of acute myeloid leukemia (AML). Sunesis is currently conducting two Phase 2 clinical trials of voreloxin in AML: a single-agent study, known as REVEAL-1, of voreloxin in newly diagnosed elderly AML patients unlikely to benefit from standard induction chemotherapy and a study evaluating voreloxin in combination with cytarabine in relapsed/refractory AML. [More]

Canadian patients have less access to the latest medicines, says report

4. November 2009 03:48
Canadian patients have less access to the latest medicines when compared to the world's developed countries, concludes a comprehensive new report released today. The Report shows Canada ranks 20th out of 25 OECD countries in public reimbursement of new drug therapies. Canada's grade of 56% is comparable with Iceland, Slovakia and Turkey. [More]

Posted in: Pharmaceutical News

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Child Neurology Foundation raises $30,000 during Infantile Spasms Awareness Week

28. October 2009 11:55
The Child Neurology Foundation (CNF) today announced that $30,000 was raised during Infantile Spasms Awareness Week (October 11-17) that will go towards researching the cause and treatment of this ultra-rare form of epilepsy. [More]

Posted in: Child Health News

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Modified NAGA: New enzyme for enzyme replacement therapy

23. October 2009 07:11
A new study uses a creative structure-based remodeling strategy to design a therapeutic protein that exhibits significant advantages over currently available treatments for a rare disease that often leads to cardiac and renal failure. The research, published by Cell Press on October 22nd in the American Journal of Human Genetics, describes a new and highly promising candidate for enzyme replacement therapy (ERT) for Fabry disease. [More]

Posted in: Medical Science News | Medical Condition News

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NCCN Guidelines for Acute Myeloid Leukemia updated

20. October 2009 05:52
The National Comprehensive Cancer Network (NCCN) recently made updates to the NCCN Clinical Practice Guidelines in Oncology(TM) for Acute Myeloid Leukemia, a cancer that starts inside the bone marrow and the most common acute leukemia affecting adults. [More]

MDS secures international cooperation to help Canadian teenager with malignant blood disorder

15. October 2009 08:07
The Myelodysplastic Syndromes (MDS) Foundation says a wide range of international cooperation has been secured to help 18-year-old Wes Laporte of Ontario get treatment for a life-threatening condition in the US. [More]

University of North Carolina awarded grant to continue research on rare disease-causing gene mutations

14. October 2009 07:03
The University of North Carolina at Chapel Hill has been awarded a five-year, $6.2 million renewal grant to continue its work as part of the National Institutes of Health's Rare Diseases Clinical Research Network (RDCRN). [More]

Posted in: Medical Science News

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CNF launches new educational website centered on infantile spasms

12. October 2009 10:55
The Child Neurology Foundation (CNF) today announced the launch of a new educational website centered on infantile spasms (IS). The website, www.infantilespasmsinfo.org, is an educational resource developed by the CNF as one of the key components of Infantile Spasms Awareness Week. [More]

Posted in: Child Health News | Device / Technology News

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Antidotes effective for treating acute liver failure patients in early stages of disease

8. October 2009 03:39
The antidote for acute liver failure caused by acetaminophen poisoning also can treat acute liver failure due to most other causes if given before severe injury occurs, UT Southwestern Medical Center researchers and their colleagues at 21 other institutions have found. [More]

Research to explore diagnosis and treatment of rare diseases

7. October 2009 03:05
The National Institutes of Health announced today a second phase of the Rare Diseases Clinical Research Network (RDCRN) including funds for 19 research consortia. [More]
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