Raptor Pharmaceutical Corp. ("Raptor" or the "Company") (Nasdaq: RPTP), today announced the presentation of cystinosis data at the Annual Lysosomal Disease Network WORLD Symposium 2010, being held February 10-12 in Miami, Florida. Biomarker data from a Phase IIb pilot study of Raptor's proprietary delayed-release cysteamine bitartrate ("DR Cysteamine") will be the subject of a poster titled, "Correlation of Plasma Cysteamine and WBC Cystine Levels at Steady State in Patients Treated with Cysteamine Bitartrate." The results will also be published in an upcoming issue of the journal Molecular Genetics and Metabolism.
The data supports the effectiveness of pre-dose plasma cysteamine concentration in determining the correct cysteamine dose for nephropathic cystinosis ("cystinosis") patients. Pre-dose plasma cysteamine concentration is an easier biomarker to measure in clinical settings compared to cystine levels in white blood cells ("WBC"s). Researchers in the pilot study found that pre-dose plasma cysteamine concentration has the potential to be a viable alternative to WBC cystine levels as a predictive biomarker for proper cysteamine dosing.