Porphyrias News and Research

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Alnylam announces positive results from Phase 3 Study of givosiran for treating acute hepatic porphyria

Alnylam announces positive results from Phase 3 Study of givosiran for treating acute hepatic porphyria

Newly-discovered mutation highlights complex genetic network that underpins blood disorder

Newly-discovered mutation highlights complex genetic network that underpins blood disorder

Rare genetic variations linked to severe porphyria

Rare genetic variations linked to severe porphyria

Photodynamic therapy effective in treating porphyrias but can be severely painful, cause inflammation

Photodynamic therapy effective in treating porphyrias but can be severely painful, cause inflammation

Alnylam announces new pre-clinical results with DC for ALN-CC5 to treat complement-mediated diseases

Alnylam announces new pre-clinical results with DC for ALN-CC5 to treat complement-mediated diseases

Alnylam advances Development Candidate for ALN-AS1 for treatment of hepatic porphyrias

Alnylam advances Development Candidate for ALN-AS1 for treatment of hepatic porphyrias

Alnylam reports pre-clinical data from ALN-AS1 program for treatment of AIP

Alnylam reports pre-clinical data from ALN-AS1 program for treatment of AIP

Medunik Canada signs exclusive distribution agreement with Orphan Europe

Medunik Canada signs exclusive distribution agreement with Orphan Europe

SCENESSE reduces, prevents phototoxic reactions experienced by EPP patients in Phase III trial

SCENESSE reduces, prevents phototoxic reactions experienced by EPP patients in Phase III trial

Research to explore diagnosis and treatment of rare diseases

Research to explore diagnosis and treatment of rare diseases

Researchers reveal basis for hereditary coproporphyria

Researchers reveal basis for hereditary coproporphyria

Molecular missing link between fasting and acute attacks of porphyria

Molecular missing link between fasting and acute attacks of porphyria