Beta Thalassemia News and Research

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Beta-thalassemia (ß-thalassemia) is a form of thalassemia due to mutations in the HBB gene on chromosome 11 , inherited in an autosomal recessive fashion.
Researchers develop proof-of-concept treatment for blood disorders

Researchers develop proof-of-concept treatment for blood disorders

Study: TALEN is five times more efficient than CRISPR-Cas9 in tightly packed DNA

Study: TALEN is five times more efficient than CRISPR-Cas9 in tightly packed DNA

New taxonomic classification of non-skeletal rare congenital disorders with impact on bone physiology

New taxonomic classification of non-skeletal rare congenital disorders with impact on bone physiology

Rice University wins prestigious grant to develop new therapies for sickle cell disease

Rice University wins prestigious grant to develop new therapies for sickle cell disease

Ancient DNA analysis provides insight into genetic history of Sardinia

Ancient DNA analysis provides insight into genetic history of Sardinia

Horizon Discovery to offer novel base editing technology for clinical research

Horizon Discovery to offer novel base editing technology for clinical research

Mystery surrounds gene edited babies one year on

Mystery surrounds gene edited babies one year on

Pioneering CRISPR therapy leaves two patients free of blood disease symptoms

Pioneering CRISPR therapy leaves two patients free of blood disease symptoms

Deterministic mechanoporation of cells en masse to cure cancer

Deterministic mechanoporation of cells en masse to cure cancer

Carnegie Mellon and Yale win NIH grant to advance gene editing technique

Carnegie Mellon and Yale win NIH grant to advance gene editing technique

Researchers make breakthrough in gene therapy for sickle cell disease

Researchers make breakthrough in gene therapy for sickle cell disease

Genetic engineering could open possibilities for patients with Parkinson’s disease

Genetic engineering could open possibilities for patients with Parkinson’s disease

Study compares effectiveness and cost of gene therapy and HSCT in major beta-thalassemia

Study compares effectiveness and cost of gene therapy and HSCT in major beta-thalassemia

Researchers develop new strategy to treat sickle cell disease and beta thalassemia

Researchers develop new strategy to treat sickle cell disease and beta thalassemia

Deadly inherited blood disorders cured with bone marrow transplant

Deadly inherited blood disorders cured with bone marrow transplant

App that could detect level of anemia by looking at fingernails

App that could detect level of anemia by looking at fingernails

Researchers identify enzyme as potential new drug target for blood disorders

Researchers identify enzyme as potential new drug target for blood disorders

Mice study shows promise for treating genetic conditions during fetal development

Mice study shows promise for treating genetic conditions during fetal development

Research project offers hope for pediatric patients with thalassemia

Research project offers hope for pediatric patients with thalassemia

Celgene to share new and updated data around novel hematological therapies

Celgene to share new and updated data around novel hematological therapies