Beta Thalassemia News and Research

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Beta-thalassemia (ß-thalassemia) is a form of thalassemia due to mutations in the HBB gene on chromosome 11 , inherited in an autosomal recessive fashion.
Genetic engineering could open possibilities for patients with Parkinson’s disease

Genetic engineering could open possibilities for patients with Parkinson’s disease

Study compares effectiveness and cost of gene therapy and HSCT in major beta-thalassemia

Study compares effectiveness and cost of gene therapy and HSCT in major beta-thalassemia

Researchers develop new strategy to treat sickle cell disease and beta thalassemia

Researchers develop new strategy to treat sickle cell disease and beta thalassemia

Deadly inherited blood disorders cured with bone marrow transplant

Deadly inherited blood disorders cured with bone marrow transplant

App that could detect level of anemia by looking at fingernails

App that could detect level of anemia by looking at fingernails

Researchers identify enzyme as potential new drug target for blood disorders

Researchers identify enzyme as potential new drug target for blood disorders

Mice study shows promise for treating genetic conditions during fetal development

Mice study shows promise for treating genetic conditions during fetal development

Research project offers hope for pediatric patients with thalassemia

Research project offers hope for pediatric patients with thalassemia

Celgene to share new and updated data around novel hematological therapies

Celgene to share new and updated data around novel hematological therapies

“Chemical surgery” on embryos to free them of a gene causing thalassemia

“Chemical surgery” on embryos to free them of a gene causing thalassemia

Metabolism can impact host's susceptibility to develop malaria

Metabolism can impact host's susceptibility to develop malaria

Study provides insight into development of red blood cells

Study provides insight into development of red blood cells

US scientists make advances in modifying human embryos

US scientists make advances in modifying human embryos

Innovative gene therapy allows complete remission of clinical signs of sickle cell disease

Innovative gene therapy allows complete remission of clinical signs of sickle cell disease

Scientists find new way to use CRISPR gene editing to help fix sickle cell disease

Scientists find new way to use CRISPR gene editing to help fix sickle cell disease

Minihepcidins may potentially treat serious genetic blood diseases in children, adults

Minihepcidins may potentially treat serious genetic blood diseases in children, adults

Sangamo presents immunological data from SB-728-T HIV clinical study at CROI 2016

Sangamo presents immunological data from SB-728-T HIV clinical study at CROI 2016

FDA clears Sangamo BioSciences' SB-318 IND application for treatment of MPS I

FDA clears Sangamo BioSciences' SB-318 IND application for treatment of MPS I

Sangamo presents Phase 2 data from two ongoing clinical trials of SB-728-T for treatment of HIV/AIDS

Sangamo presents Phase 2 data from two ongoing clinical trials of SB-728-T for treatment of HIV/AIDS

Experimental gene therapy may improve health outcomes for patients with some forms of blood disorders

Experimental gene therapy may improve health outcomes for patients with some forms of blood disorders