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New approach using RNA therapeutic can fix protein problems in cystic fibrosis

New approach using RNA therapeutic can fix protein problems in cystic fibrosis

Study finds evidence to strongly implicate OAS1 as an effector gene influencing COVID-19 severity

Study finds evidence to strongly implicate OAS1 as an effector gene influencing COVID-19 severity

Virus-like particles as delivery vehicles for gene-editing

Virus-like particles as delivery vehicles for gene-editing

SARS-CoV-2 levels decrease when human SIRT5 is deleted or inhibited

SARS-CoV-2 levels decrease when human SIRT5 is deleted or inhibited

Study shows long-term safety and biologic activity of golodirsen in DMD patients

Study shows long-term safety and biologic activity of golodirsen in DMD patients

Researchers identify mechanism behind regulation of large exon splicing during vertebrate evolution

Researchers identify mechanism behind regulation of large exon splicing during vertebrate evolution

Osimertinib offers a hint of added benefit for NSCLC patients who have received adjuvant chemotherapy

Osimertinib offers a hint of added benefit for NSCLC patients who have received adjuvant chemotherapy

AI technique could lead to new ways to predict cancer prognosis and treatment response

AI technique could lead to new ways to predict cancer prognosis and treatment response

Grouping EGFR mutations provides an accurate way to match lung cancer patients to the right drugs

Grouping EGFR mutations provides an accurate way to match lung cancer patients to the right drugs

Study identifies actionable genes and candidate drugs in biliary tract cancer using a knowledgebase

Study identifies actionable genes and candidate drugs in biliary tract cancer using a knowledgebase

New study identifies novel compound as promising pan-coronavirus drug candidate

New study identifies novel compound as promising pan-coronavirus drug candidate

Potential new treatment for mast cell cancers reduces tumor size and prevents organ infiltration

Potential new treatment for mast cell cancers reduces tumor size and prevents organ infiltration

New study describes SARS-CoV-2 ExoN enzyme that promotes antiviral resistance

New study describes SARS-CoV-2 ExoN enzyme that promotes antiviral resistance

New components for oligonucleotide drugs show safety, efficacy in treating spinal muscular atrophy

New components for oligonucleotide drugs show safety, efficacy in treating spinal muscular atrophy

Study explores the potential role of gene polymorphisms in pathogenesis of prostate cancer

Study explores the potential role of gene polymorphisms in pathogenesis of prostate cancer

Researchers create the most comprehensive atlas of human transcriptome

Researchers create the most comprehensive atlas of human transcriptome

Leducq Foundation  provides $7 million to support Cardiac Splicing as a Therapeutic Target project

Leducq Foundation provides $7 million to support Cardiac Splicing as a Therapeutic Target project

New bioengineered reporter system allows to follow protein isoform expression over time in live cells

New bioengineered reporter system allows to follow protein isoform expression over time in live cells

FDA approves Rybrevant for treating subset of non-small cell lung cancer

FDA approves Rybrevant for treating subset of non-small cell lung cancer

New gene therapy restores dystrophin protein in patients with Duchenne muscular dystrophy

New gene therapy restores dystrophin protein in patients with Duchenne muscular dystrophy