Sandhoff Disease News and Research

RSS
Gene therapy is the best stratagem to impact the course of GM2 gangliosidosis

Gene therapy is the best stratagem to impact the course of GM2 gangliosidosis

Researchers describe important step toward gene therapy for patients with Sandhoff disease

Researchers describe important step toward gene therapy for patients with Sandhoff disease

Genetic therapy for two inherited neurologic diseases moves closer to human clinical trials

Genetic therapy for two inherited neurologic diseases moves closer to human clinical trials

Stem cells delay neurodegeneration in the brain

Stem cells delay neurodegeneration in the brain

Infants with Krabbe disease saved by cord blood stem cells

Infants with Krabbe disease saved by cord blood stem cells