Hemophilia News and Research

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Hemophilia is a rare, inherited bleeding disorder in which your blood doesn’t clot normally. If you have hemophilia, you may bleed for a longer time than others after an injury. You also may bleed internally, especially in your knees, ankles, and elbows. This bleeding can damage your organs or tissues and, sometimes, be fatal.
MOFs could help improve the delivery of genetic cargo into target cells

MOFs could help improve the delivery of genetic cargo into target cells

Immunobridging study shows immunogenicity in adolescents receiving SARS-CoV-2 mRNA and inactivated vaccines

Immunobridging study shows immunogenicity in adolescents receiving SARS-CoV-2 mRNA and inactivated vaccines

Researchers secure $12 million grant to develop improved therapies for hemophilia

Researchers secure $12 million grant to develop improved therapies for hemophilia

Dexamethasone administration at a late time point could enhance transgene expression

Dexamethasone administration at a late time point could enhance transgene expression

Study determines minimally effective dose of clinical candidate gene therapy vector to treat hemophilia A

Study determines minimally effective dose of clinical candidate gene therapy vector to treat hemophilia A

What does the future look like for bleeding disorders?

What does the future look like for bleeding disorders?

TXA drug has minimal impact in controlling blood loss in severely injured trauma patients

TXA drug has minimal impact in controlling blood loss in severely injured trauma patients

New trial demonstrates stable coagulation factor VIII in hemophilia A patients after gene therapy

New trial demonstrates stable coagulation factor VIII in hemophilia A patients after gene therapy

Why we may never know whether the $56,000-a-year Alzheimer’s drug actually works

Why we may never know whether the $56,000-a-year Alzheimer’s drug actually works

New approach to gene therapy uses common pain reliever to fight against genetic diseases

New approach to gene therapy uses common pain reliever to fight against genetic diseases

Immune tolerance in hemophilia can be modulated by B cell activating factor

Immune tolerance in hemophilia can be modulated by B cell activating factor

CHOP researchers identify key target responsible for treatment failure in patients with hemophilia A

CHOP researchers identify key target responsible for treatment failure in patients with hemophilia A

Spark Therapeutics launches gene therapy clinical trial for late-onset Pompe disease

Spark Therapeutics launches gene therapy clinical trial for late-onset Pompe disease

New taxonomic classification of non-skeletal rare congenital disorders with impact on bone physiology

New taxonomic classification of non-skeletal rare congenital disorders with impact on bone physiology

New clinical practice guidelines on diagnosis, management of von Willebrand Disease

New clinical practice guidelines on diagnosis, management of von Willebrand Disease

NIH-funded study to test emergency treatment for devastating stroke in Memphis

NIH-funded study to test emergency treatment for devastating stroke in Memphis

Providing personalized care for bleeding disorders

Providing personalized care for bleeding disorders

Providing personalized care for bleeding disorders

Providing personalized care for bleeding disorders

Shielding stem cells with novel biomaterial can reduce heart attack damage

Shielding stem cells with novel biomaterial can reduce heart attack damage

New articles focus on recent developments in the field of health preference research

New articles focus on recent developments in the field of health preference research