Hemophilia News and Research

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Hemophilia is a rare, inherited bleeding disorder in which your blood doesn’t clot normally. If you have hemophilia, you may bleed for a longer time than others after an injury. You also may bleed internally, especially in your knees, ankles, and elbows. This bleeding can damage your organs or tissues and, sometimes, be fatal.
FDA advisory committee vote 16-0 for first even gene therapy for rare blindness

FDA advisory committee vote 16-0 for first even gene therapy for rare blindness

TSRI study offers key insights into possible links between sleep and hunger

TSRI study offers key insights into possible links between sleep and hunger

TSRI scientists demonstrate repurposing of DNA to create new substances

TSRI scientists demonstrate repurposing of DNA to create new substances

New microcapsules represent promising vectors for application of genome-editing tools

New microcapsules represent promising vectors for application of genome-editing tools

TSRI scientists find new approach to reprogram ordinary adult cells into IPSCs

TSRI scientists find new approach to reprogram ordinary adult cells into IPSCs

Pfizer announces launch two new digital innovations to help people living with hemophilia

Pfizer announces launch two new digital innovations to help people living with hemophilia

Shire partners with MicroHealth to support secure care monitoring tool for hemophilia patients with inhibitors

Shire partners with MicroHealth to support secure care monitoring tool for hemophilia patients with inhibitors

Researchers visually capture 'shapeshifter' that regulates blood clotting

Researchers visually capture 'shapeshifter' that regulates blood clotting

Researchers investigate genetic mutations in sperm cells to help prevent birth defects

Researchers investigate genetic mutations in sperm cells to help prevent birth defects

FDA approves new combo drug Mavyret for adults with Hepatitis C infection

FDA approves new combo drug Mavyret for adults with Hepatitis C infection

Gene-therapy administered through skin transplants could enable treatment of many diseases

Gene-therapy administered through skin transplants could enable treatment of many diseases

In Massachusetts, proposed Medicaid cuts put kids’ health care at risk

In Massachusetts, proposed Medicaid cuts put kids’ health care at risk

Novel therapy decreases incidence of bleeding by 87% in hemophilia A patients with inhibitors

Novel therapy decreases incidence of bleeding by 87% in hemophilia A patients with inhibitors

Abbott introduces Sekisui CP3000 fully automated coagulation system for accurate test results

Abbott introduces Sekisui CP3000 fully automated coagulation system for accurate test results

International team to set how gene therapies in hemophilia should be measured for effectiveness

International team to set how gene therapies in hemophilia should be measured for effectiveness

TSRI scientist and partners receive $7.2 million grant to create new RNA-based treatments for ALS

TSRI scientist and partners receive $7.2 million grant to create new RNA-based treatments for ALS

Altered virus could help more patients to become eligible for human gene therapy trials

Altered virus could help more patients to become eligible for human gene therapy trials

TSRI scientists solve cellular mystery that may have implications for fundamental biology

TSRI scientists solve cellular mystery that may have implications for fundamental biology

Anti-heroin vaccine developed at TSRI proven effective in primate models

Anti-heroin vaccine developed at TSRI proven effective in primate models

TSRI study reveals first-ever structure of Lassa virus protein

TSRI study reveals first-ever structure of Lassa virus protein