Leber Congenital Amaurosis News and Research

RSS
Preclinical data of Ocugen's OCU400 genetic modifier published in Nature Gene Therapy

Preclinical data of Ocugen's OCU400 genetic modifier published in Nature Gene Therapy

Gene-editing technique CRISPR trialed for first time as cancer treatment

Gene-editing technique CRISPR trialed for first time as cancer treatment

Fight for Sight launches campaign to highlight impact of sight loss and possibilities of eye research

Fight for Sight launches campaign to highlight impact of sight loss and possibilities of eye research

Johns Hopkins researchers develop new way to deliver sight-saving gene therapy to the retina

Johns Hopkins researchers develop new way to deliver sight-saving gene therapy to the retina

7-year-old treated with FDA-approved gene therapy for Leber congenital amaurosis

7-year-old treated with FDA-approved gene therapy for Leber congenital amaurosis

New therapy for childhood blindness shows 'very promising' results

New therapy for childhood blindness shows 'very promising' results

Intraocular injection improves vision in a form of congenital retinal blindness

Intraocular injection improves vision in a form of congenital retinal blindness

Gene therapy for rare genetic blindness wins prestigious Champalimaud Vision award

Gene therapy for rare genetic blindness wins prestigious Champalimaud Vision award

Study finds genetic treatment for inherited retinal disorder

Study finds genetic treatment for inherited retinal disorder

New gene therapy for blindness may soon be reality

New gene therapy for blindness may soon be reality

FDA advisory committee vote 16-0 for first even gene therapy for rare blindness

FDA advisory committee vote 16-0 for first even gene therapy for rare blindness

Suppression of thyroid hormone receptor protects cone cells in mouse models of retinal diseases

Suppression of thyroid hormone receptor protects cone cells in mouse models of retinal diseases

OIST scientists use zebrafish model to unravel causes behind human LCA

OIST scientists use zebrafish model to unravel causes behind human LCA

Penn scientists find striking similarities between human patients with LCA and dogs

Penn scientists find striking similarities between human patients with LCA and dogs

Study shows children with rare eye disease have greatest benefit from gene therapy

Study shows children with rare eye disease have greatest benefit from gene therapy

Gene therapy restores visual function in mouse model of LCA1

Gene therapy restores visual function in mouse model of LCA1

Genetic finding could lead to new treatments for people living with blindness, vision loss

Genetic finding could lead to new treatments for people living with blindness, vision loss

Auxilium Pharmaceuticals plans to merge with QLT

Auxilium Pharmaceuticals plans to merge with QLT

Human Treg responses allow sustained recombinant adeno-associated virus-mediated transgene expression

Human Treg responses allow sustained recombinant adeno-associated virus-mediated transgene expression

Investigators report complete catalog of genes expressed in retina

Investigators report complete catalog of genes expressed in retina