Leber Congenital Amaurosis News and Research

RSS
Gene therapy for common forms of congenital blindness shows promise to improve vision

Gene therapy for common forms of congenital blindness shows promise to improve vision

Single injection of RNA therapy improves vision in patient with genetic form of childhood blindness

Single injection of RNA therapy improves vision in patient with genetic form of childhood blindness

Gene therapy restores vison in dogs with severe form of Leber congenital amaurosis

Gene therapy restores vison in dogs with severe form of Leber congenital amaurosis

NEI scientists develop and test a promising gene therapy strategy for rare eye disease

NEI scientists develop and test a promising gene therapy strategy for rare eye disease

Large study provides new understanding of genome diversity in Ukrainian population

Large study provides new understanding of genome diversity in Ukrainian population

Study uncovers a promising therapeutic target for retinal dystrophies

Study uncovers a promising therapeutic target for retinal dystrophies

Newly developed light-sensing protein restores vision in blind mice

Newly developed light-sensing protein restores vision in blind mice

Study helps restore retinal and visual functions of mice models of inherited retinal disease

Study helps restore retinal and visual functions of mice models of inherited retinal disease

Preclinical data of Ocugen's OCU400 genetic modifier published in Nature Gene Therapy

Preclinical data of Ocugen's OCU400 genetic modifier published in Nature Gene Therapy

Gene-editing technique CRISPR trialed for first time as cancer treatment

Gene-editing technique CRISPR trialed for first time as cancer treatment

Fight for Sight launches campaign to highlight impact of sight loss and possibilities of eye research

Fight for Sight launches campaign to highlight impact of sight loss and possibilities of eye research

Johns Hopkins researchers develop new way to deliver sight-saving gene therapy to the retina

Johns Hopkins researchers develop new way to deliver sight-saving gene therapy to the retina

7-year-old treated with FDA-approved gene therapy for Leber congenital amaurosis

7-year-old treated with FDA-approved gene therapy for Leber congenital amaurosis

New therapy for childhood blindness shows 'very promising' results

New therapy for childhood blindness shows 'very promising' results

Intraocular injection improves vision in a form of congenital retinal blindness

Intraocular injection improves vision in a form of congenital retinal blindness

Gene therapy for rare genetic blindness wins prestigious Champalimaud Vision award

Gene therapy for rare genetic blindness wins prestigious Champalimaud Vision award

Study finds genetic treatment for inherited retinal disorder

Study finds genetic treatment for inherited retinal disorder

New gene therapy for blindness may soon be reality

New gene therapy for blindness may soon be reality

FDA advisory committee vote 16-0 for first even gene therapy for rare blindness

FDA advisory committee vote 16-0 for first even gene therapy for rare blindness

Suppression of thyroid hormone receptor protects cone cells in mouse models of retinal diseases

Suppression of thyroid hormone receptor protects cone cells in mouse models of retinal diseases