Neuromuscular Disease News and Research

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International experts to gather for ALS symposium in Chicago

International experts to gather for ALS symposium in Chicago

Eliminating race adjustment in lung function tests may alter diagnosis and disability eligibility

Eliminating race adjustment in lung function tests may alter diagnosis and disability eligibility

Real-world data validates gene therapy for spinal muscular atrophy

Real-world data validates gene therapy for spinal muscular atrophy

Patient-specific muscle models pave way for personalized neuromuscular therapies

Patient-specific muscle models pave way for personalized neuromuscular therapies

First successful Phase 2 trial uses cutting-edge RNA CAR-T therapy to treat autoimmunity

First successful Phase 2 trial uses cutting-edge RNA CAR-T therapy to treat autoimmunity

Using human iPSC-derived cells to revolutionize the field of neurodegenerative disease

Using human iPSC-derived cells to revolutionize the field of neurodegenerative disease

Vaccines and monoclonal antibodies being developed for respiratory syncytial virus

Vaccines and monoclonal antibodies being developed for respiratory syncytial virus

UT Southwestern researchers reveal the physical mechanism behind a neurological autoimmune disease

UT Southwestern researchers reveal the physical mechanism behind a neurological autoimmune disease

New consensus-based recommendations designed to improve quality of life for DMD patients

New consensus-based recommendations designed to improve quality of life for DMD patients

Identifying an important protein for motor coordination

Identifying an important protein for motor coordination

Study reveals the role of SPOP protein in an inherited form of ALS

Study reveals the role of SPOP protein in an inherited form of ALS

A new 3D model for myotonic dystrophy

A new 3D model for myotonic dystrophy

Spark Therapeutics launches gene therapy clinical trial for late-onset Pompe disease

Spark Therapeutics launches gene therapy clinical trial for late-onset Pompe disease

Canadian Neuromuscular Disease Registry increases patient access to research, clinical trials

Canadian Neuromuscular Disease Registry increases patient access to research, clinical trials

Genethon to start international clinical trial for treatment of Duchenne muscular dystrophy

Genethon to start international clinical trial for treatment of Duchenne muscular dystrophy

Researchers identify new strategy to combat loss of skeletal muscle mass

Researchers identify new strategy to combat loss of skeletal muscle mass

Study offers renewed hope for children suffering from myofibrillar myopathies

Study offers renewed hope for children suffering from myofibrillar myopathies

New drug offers hope for young boys with Duchenne muscular dystrophy

New drug offers hope for young boys with Duchenne muscular dystrophy

Study implicates new gene as driver of motor neuron diseases

Study implicates new gene as driver of motor neuron diseases

Researchers find link between dystrophic muscles and lymphatic system in mice with Duchenne disease

Researchers find link between dystrophic muscles and lymphatic system in mice with Duchenne disease

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