Neuromuscular Disease News and Research

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A new 3D model for myotonic dystrophy

A new 3D model for myotonic dystrophy

Spark Therapeutics launches gene therapy clinical trial for late-onset Pompe disease

Spark Therapeutics launches gene therapy clinical trial for late-onset Pompe disease

Canadian Neuromuscular Disease Registry increases patient access to research, clinical trials

Canadian Neuromuscular Disease Registry increases patient access to research, clinical trials

Genethon to start international clinical trial for treatment of Duchenne muscular dystrophy

Genethon to start international clinical trial for treatment of Duchenne muscular dystrophy

Researchers identify new strategy to combat loss of skeletal muscle mass

Researchers identify new strategy to combat loss of skeletal muscle mass

Study offers renewed hope for children suffering from myofibrillar myopathies

Study offers renewed hope for children suffering from myofibrillar myopathies

New drug offers hope for young boys with Duchenne muscular dystrophy

New drug offers hope for young boys with Duchenne muscular dystrophy

Study implicates new gene as driver of motor neuron diseases

Study implicates new gene as driver of motor neuron diseases

Researchers find link between dystrophic muscles and lymphatic system in mice with Duchenne disease

Researchers find link between dystrophic muscles and lymphatic system in mice with Duchenne disease

Study examines safety and early outcomes of gene therapy for spinal muscular atrophy

Study examines safety and early outcomes of gene therapy for spinal muscular atrophy

Study fills crucial knowledge gaps on myasthenia gravis

Study fills crucial knowledge gaps on myasthenia gravis

UOttawa's Faculty of Medicine awards 58 clinical research chairs to top clinician-scientists

UOttawa's Faculty of Medicine awards 58 clinical research chairs to top clinician-scientists

Curi Bio Acquires Dana Solutions

Curi Bio Acquires Dana Solutions

Researchers identify new molecules to study specific glial cells integral to synapses

Researchers identify new molecules to study specific glial cells integral to synapses

Micro-dystrophin gene therapy can improve outcomes in children with Duchenne muscular dystrophy

Micro-dystrophin gene therapy can improve outcomes in children with Duchenne muscular dystrophy

Antisense Therapeutics: Poster presentation on the Muscular Dystrophy Association Virtual Conference 2020 website

Antisense Therapeutics: Poster presentation on the Muscular Dystrophy Association Virtual Conference 2020 website

Researchers identify novel cellular entry factor for AAV vector types

Researchers identify novel cellular entry factor for AAV vector types

Online decision aid provides more knowledge about the benefits of genomic sequencing

Online decision aid provides more knowledge about the benefits of genomic sequencing

Tailored T-cells safe, may be effective in preventing and treating multiple viral infections

Tailored T-cells safe, may be effective in preventing and treating multiple viral infections

Molecular gatekeepers that regulate calcium ions vital for muscle health and repair

Molecular gatekeepers that regulate calcium ions vital for muscle health and repair