Muscular Dystrophy News and Research

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The muscular dystrophies (MD) are a group of more than 30 genetic diseases characterized by progressive weakness and degeneration of the skeletal muscles that control movement. Some forms of MD are seen in infancy or childhood, while others may not appear until middle age or later. The disorders differ in terms of the distribution and extent of muscle weakness (some forms of MD also affect cardiac muscle), age of onset, rate of progression, and pattern of inheritance.
UCLA researchers discover compound that stimulates muscle cells in mice

UCLA researchers discover compound that stimulates muscle cells in mice

Leaking components from broken muscle fibers activate 'satellite' muscle stem cells

Leaking components from broken muscle fibers activate 'satellite' muscle stem cells

Study elucidates the role of ERβ in growth of skeletal muscle in female mice

Study elucidates the role of ERβ in growth of skeletal muscle in female mice

Biodegradable microneedle patch for local therapeutic gene delivery

Biodegradable microneedle patch for local therapeutic gene delivery

NIH awards grants for using bioengineered models to improve clinical trial design

NIH awards grants for using bioengineered models to improve clinical trial design

New drug offers hope for young boys with Duchenne muscular dystrophy

New drug offers hope for young boys with Duchenne muscular dystrophy

Curi Bio Announces Mantarray™ Platform for Analysis of 3D Engineered Muscle Tissues for Discovery of New Therapeutics

Curi Bio Announces Mantarray™ Platform for Analysis of 3D Engineered Muscle Tissues for Discovery of New Therapeutics

Study uncovers a promising new therapeutic approach for Duchenne muscular dystrophy

Study uncovers a promising new therapeutic approach for Duchenne muscular dystrophy

RCas9 gene therapy clears toxic RNA buildup in mouse model of myotonic dystrophy

RCas9 gene therapy clears toxic RNA buildup in mouse model of myotonic dystrophy

Yale researchers identify possible treatment for Duchenne muscular dystrophy

Yale researchers identify possible treatment for Duchenne muscular dystrophy

Scientists solve decades old mystery of key molecule that fuels mitochondria

Scientists solve decades old mystery of key molecule that fuels mitochondria

Researchers find link between dystrophic muscles and lymphatic system in mice with Duchenne disease

Researchers find link between dystrophic muscles and lymphatic system in mice with Duchenne disease

FDA approves new treatment option for patients with rare Duchenne muscular dystrophy mutation

FDA approves new treatment option for patients with rare Duchenne muscular dystrophy mutation

Heart cell treatment can benefit patients, shows study

Heart cell treatment can benefit patients, shows study

C-Path gets positive response from FDA for drug-induced skeletal muscle injury safety biomarkers

C-Path gets positive response from FDA for drug-induced skeletal muscle injury safety biomarkers

Erectile dysfunction drugs lower the accumulation of toxic proteins in zebrafish models

Erectile dysfunction drugs lower the accumulation of toxic proteins in zebrafish models

Scientific evidence shows GLDH is a safe biomarker for drug-induced liver injury

Scientific evidence shows GLDH is a safe biomarker for drug-induced liver injury

Researchers use gene-editing techniques to visualize protein action in multicellular animals

Researchers use gene-editing techniques to visualize protein action in multicellular animals

Experimental drug for rare ALS shows promise in early clinical trial

Experimental drug for rare ALS shows promise in early clinical trial

New editorial published following adverse events of gene therapy clinical trial

New editorial published following adverse events of gene therapy clinical trial