Muscular Dystrophy News and Research

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The muscular dystrophies (MD) are a group of more than 30 genetic diseases characterized by progressive weakness and degeneration of the skeletal muscles that control movement. Some forms of MD are seen in infancy or childhood, while others may not appear until middle age or later. The disorders differ in terms of the distribution and extent of muscle weakness (some forms of MD also affect cardiac muscle), age of onset, rate of progression, and pattern of inheritance.
‘Why do we always get hit first?’ Proposed budget cuts target vulnerable Californians

‘Why do we always get hit first?’ Proposed budget cuts target vulnerable Californians

Using gene therapy to help the body to make its own cancer drugs

Using gene therapy to help the body to make its own cancer drugs

Study provides groundwork for restoring nerve-muscle connection in ALS

Study provides groundwork for restoring nerve-muscle connection in ALS

UTSW/Children's Health joint program approved as Certified Duchenne Care Center

UTSW/Children's Health joint program approved as Certified Duchenne Care Center

Scientists identify key cell signaling pathway that drives muscle loss

Scientists identify key cell signaling pathway that drives muscle loss

Gene therapy helps build muscle mass and reduces severity of osteoarthritis in mice

Gene therapy helps build muscle mass and reduces severity of osteoarthritis in mice

Scripps professor receives Research Program Award for advancing RNA-targeting medicines

Scripps professor receives Research Program Award for advancing RNA-targeting medicines

New study indicates novel therapies for Duchenne muscular dystrophy

New study indicates novel therapies for Duchenne muscular dystrophy

Temple researchers reverse muscle fibrosis associated with overuse injury in animals

Temple researchers reverse muscle fibrosis associated with overuse injury in animals

Model that sheds light on severe Duchenne muscular dystrophy could pave the way for new therapies

Model that sheds light on severe Duchenne muscular dystrophy could pave the way for new therapies

Finding new treatments for muscular dystrophy with CRISPR-Cas9

Finding new treatments for muscular dystrophy with CRISPR-Cas9

New form of gene editing slows ALS progression in mice

New form of gene editing slows ALS progression in mice

A promising new oral therapy to speed up healing of broken bones

A promising new oral therapy to speed up healing of broken bones

Small molecules may open the door to new therapies for Duchenne muscular dystrophy

Small molecules may open the door to new therapies for Duchenne muscular dystrophy

Study reveals molecular pathogenesis of muscular dystrophy-associated cardiomyopathy

Study reveals molecular pathogenesis of muscular dystrophy-associated cardiomyopathy

Simple accelerometers improve diagnosis of Duchenne muscular dystrophy

Simple accelerometers improve diagnosis of Duchenne muscular dystrophy

Study uncovers molecular mechanism that triggers a rare type of muscular dystrophy

Study uncovers molecular mechanism that triggers a rare type of muscular dystrophy

New gene correction therapy for hereditary muscular disease among children

New gene correction therapy for hereditary muscular disease among children

Asian parents with terminally ill children may not share psychological pain with their spouses

Asian parents with terminally ill children may not share psychological pain with their spouses

PerkinElmer provides newborn screening assay for PPMD’s New York State pilot program

PerkinElmer provides newborn screening assay for PPMD’s New York State pilot program