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European Commission grants marketing authorization for NEZGLYAL® (leriglitazone), the first pharmacological treatment approved for cerebral adrenoleukodystrophy (cALD), a rare neurodegenerative disease

Neuraxpharm Group and Minoryx Therapeutics, today announce that the European Commission (EC) has granted marketing authorization under exceptional circumstances for NEZGLYAL® (leriglitazone), an orally bioavailable, brain penetrating, selective PPAR gamma agonist, as a treatment for male cALD patients, aged 2-12 years with Gadolinium (Gd)-negative brain lesions.

26 Sep 2026

Cornell researchers document first case of Marfan syndrome in cats

Researchers at Cornell University have documented the first molecular characterization of Marfan syndrome in domestic cats in a paper in Scientific Reports.

25 Sep 2026

Uterus transplantation shows improving outcomes and successful births nationwide

A decade of uterus transplantation in the United States has resulted in dozens of healthy births and steadily improving surgical outcomes, according to a new national review led by researchers from the Perelman School of Medicine at the University of Pennsylvania.

24 Sep 2026

Study reveals why women with PCOS struggle to maintain healthy habits

A recent study in the Journal of Nutrition Education and Behavior (JNEB), published by Elsevier, provides new insight into how women with polycystic ovary syndrome (PCOS) adopt and maintain healthy eating and physical activity behaviors.

24 Sep 2026

GLP-1 drugs may influence chronic pain through gut-brain and immune pathways

Researchers reviewed evidence linking GLP-1 and GLP-1 receptor agonists to chronic pain modulation through gut microbial, neuroimmune, vagal, and metabolic pathways, with the strongest clinical evidence currently involving knee osteoarthritis and idiopathic intracranial hypertension headache. Much of the proposed biology remains supported by preclinical research, and human studies have yet to establish that GLP-1RA-induced changes in the gut microbiome directly cause pain relief.

24 Sep 2026

Sudden unexpected infant deaths drive widening Black-white mortality gap

After years of declines in sudden unexpected infant deaths (SUID), rates have been ticking up again, particularly among babies born to Black mothers, new research shows.

23 Sep 2026

Study finds oral hormone replacement therapy increases venous thromboembolism risk

Current use of oral menopausal hormone therapy (commonly known as hormone replacement therapy or HRT) is associated with an increased risk of blood clots in legs / lungs regardless of dose or treatment duration, finds a large Danish study published by The BMJ today.

23 Sep 2026

Early treatment may improve outcomes in Shwachman-Diamond syndrome

More than 90% of children born with the rare bone marrow condition called Shwachman-Diamond Syndrome (SDS) survive beyond age 20. But fewer than 30% live beyond age 50.

23 Sep 2026

Voluntary exercise reduces stress-linked bladder pain and urinary frequency

Chronic stress may contribute to the pain and urinary symptoms experienced by people with interstitial cystitis/bladder pain syndrome (IC/BPS) by triggering changes in the bladder and nervous system, according to a preclinical study by Weill Cornell Medicine investigators.

23 Sep 2026

New study highlights difficulty of detecting gastric ulcer pain in horses

A new study led by Australian veterinarians has exposed the challenge of identifying pain in horses with gastric ulcers and highlights an urgent need to better detect when horses are suffering.

23 Sep 2026

Higher ultra-processed food intake linked to multiple health risks

A higher ultra processed food (UPF) intake is linked to a heightened risk of several major chronic health issues, such as digestive diseases, high blood pressure, and metabolic syndrome/diabetes, as well as death, finds a pooled data analysis of the available evidence, published in the open access journal Family Medicine and Community Health.

22 Sep 2026

C-Path awards $1.7 million to advance five drug development projects

Critical Path Institute (C-Path) today announced that its Translational Therapeutics Accelerator has awarded $1,699,500 through five Bridging Research and Innovation in Drug Development Grants (BRIDGe).

22 Sep 2026

Low spinal bone density may predict faster brain aging

Researchers at Johns Hopkins University found that lower bone mineral density in the spine was associated with faster cognitive decline and accelerated age-related white matter injury, according to a new study published today in Radiology, a journal of the Radiological Society of North America.

22 Sep 2026

New spin-out launches technology to revolutionize hormone disorder diagnosis

The University of Birmingham and Imperial College London have announced the launch of Intelligent Mass Spec Solutions Ltd (IMS Solutions), a new spin-out that is set to revolutionize diagnosis of conditions featuring disordered steroid hormone metabolism.

22 Sep 2026

High cognitive impairment rates among homeless people demand radical policy change

Cognitive impairment is a prevalent but often unaddressed factor in chronic homelessness, and it must be addressed to help reduce homelessness, argues the author of a commentary published in CMAJ

21 Sep 2026

Daily vitamin C may benefit pre-cancerous blood disorder patients

Vitamin C is an essential nutrient that supports immune function, promotes wound healing and protects cells from molecular damage.

21 Sep 2026

HIV awareness emphasizes prevention, treatment and healthy aging

About 1.2 million people in the United States are living with HIV, or human immunodeficiency virus. Because of major advances in medical treatment and technology, people with HIV are living long, healthy lives.

18 Sep 2026

Otolaryngologists gather to present latest advances in ear, nose, and throat care

The latest treatments and research advances in ear, nose, and throat care will take center stage in Los Angeles October 17-20, when more than 5,000 of the world's leading otolaryngologists gather for the 2026 Annual Meeting & OTO EXPO of the American Academy of Otolaryngology–Head and Neck Surgery Foundation.

18 Sep 2026

New clues link Long COVID and POTS

Dizziness, fatigue, brain fog and a racing heart. They’re commonly associated with Long COVID, but new Adelaide University research suggests that for some people, these symptoms may also be indications of Postural orthostatic tachycardia syndrome (POTS), a debilitating and difficult-to-diagnose condition.

18 Sep 2026

Sex-specific biological clocks reveal how aging differs across the body in women and men

Researchers developed 38 sex-specific biological aging clocks across 15 organ systems, finding differences between females and males in genetic architecture, molecular signatures, disease associations, and mortality patterns. Brain aging clocks were linked to progression from mild cognitive impairment to Alzheimer’s disease in both sexes and to sex-dependent cognitive trajectories among solanezumab-treated A4 participants, while the authors stressed that sex-pooled and sex-interaction models remain complementary approaches.

17 Sep 2026