Neuromuscular Disease News and Research

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UOttawa's Faculty of Medicine awards 58 clinical research chairs to top clinician-scientists

The Faculty of Medicine has awarded 58 clinical research chairs to top clinician-scientists in a five-year, $40 million investment to drive clinical research excellence and enhance health and patient care.

30 Jul 2020

Curi Bio Acquires Dana Solutions

Curi Bio has acquired Dana Solutions, a pioneer in the application of artificial intelligence and machine learning to in vitro cell-based assays.

From Curi Bio 27 Jul 2020

Researchers identify new molecules to study specific glial cells integral to synapses

While the brain is composed of two types of cells, glia tend to receive far less attention for their importance in brain function and disease than the more celebrated neurons.

26 Jun 2020

Micro-dystrophin gene therapy can improve outcomes in children with Duchenne muscular dystrophy

Researchers from Nationwide Children's Hospital have published in JAMA Neurology results from the first four patients treated in the first clinical trial of systemic delivery of micro-dystrophin gene therapy in children with Duchenne muscular dystrophy (DMD) - and initial findings suggest that the therapy can provide functional improvement that is greater than that observed under the standard of care.

16 Jun 2020

Antisense Therapeutics: Poster presentation on the Muscular Dystrophy Association Virtual Conference 2020 website

Antisense Therapeutics, an Australian biopharmaceutical company developing and commercializing antisense pharmaceuticals for unmet need in rare diseases announces a virtual poster presentation on the Muscular Dystrophy Association Virtual 2020 Conference website.

15 Jun 2020

Researchers identify novel cellular entry factor for AAV vector types

Researchers led by a team at Massachusetts Eye and Ear have identified a novel cellular entry factor for adeno-associated virus vector (AAV) types--the most commonly used viral vectors for in vivo gene therapy. AAVs are vectors-or vehicles--that are created from a virus that is made harmless by molecular engineering, and have shown promise transporting genetic therapy treatments to affected tissues.

23 Jan 2020

Online decision aid provides more knowledge about the benefits of genomic sequencing

A decision aid developed to support patients undergoing genomic sequencing can reduce the amount of time patients spend speaking with overburdened genetic counselors while helping them were more knowledgeable about the benefits of sequencing, suggests a study from St. Michael's Hospital.

10 Dec 2019

Tailored T-cells safe, may be effective in preventing and treating multiple viral infections

Tailored T-cells specially designed to combat a half dozen viruses are safe and may be effective in preventing and treating multiple viral infections, according to research led by Children's National Hospital faculty.

18 Nov 2019

Molecular gatekeepers that regulate calcium ions vital for muscle health and repair

Calcium ions are essential to how muscles work effectively, playing a starring role in how and when muscles contract, tap energy stores to keep working and self-repair damage.

31 Oct 2019

A young woman, a wheelchair and the fight to take her place at Stanford

Sylvia Colt-Lacayo is 18, fresh-faced and hopeful, as she beams confidence from her power wheelchair. Her long dark hair is soft and carefully tended, and her wide brown eyes are bright.

4 Sep 2019

Resveratrol found in grapes could help astronauts on Mars

For the first humans on landing on Mars, a natural ingredient resveratrol could help prevent muscle atrophy due to zero gravity says a report in the Frontiers in Physiology.

18 Jul 2019

New drug provides hope for patients with Duchenne muscular dystrophy

The results from three clinical trials have shown that a new drug can successfully delay the progression of Duchenne muscular dystrophy.

10 Jul 2019

Researchers identify previously unknown autoimmune disease involving muscle pain, weakness

A previously unknown autoimmune muscle disease involving sudden onset of debilitating muscle pain and weakness has been identified by researchers at Washington University School of Medicine in St. Louis.

3 Jun 2019

Lithium improves muscle size and strength in mice with limb girdle muscular dystrophy

Standing up from a chair, climbing stairs, brushing one's hair - all can be a struggle for people with a rare form of muscular dystrophy that causes progressive weakness in the shoulders and hips. Over time, many such people lose the ability to walk or to lift their arms above their heads.

3 Jun 2019

Neuromuscular Disease News and Research

UOttawa's Faculty of Medicine awards 58 clinical research chairs to top clinician-scientists

Curi Bio Acquires Dana Solutions

Researchers identify new molecules to study specific glial cells integral to synapses

Micro-dystrophin gene therapy can improve outcomes in children with Duchenne muscular dystrophy

Antisense Therapeutics: Poster presentation on the Muscular Dystrophy Association Virtual Conference 2020 website

Researchers identify novel cellular entry factor for AAV vector types

Online decision aid provides more knowledge about the benefits of genomic sequencing

Tailored T-cells safe, may be effective in preventing and treating multiple viral infections

Molecular gatekeepers that regulate calcium ions vital for muscle health and repair

A young woman, a wheelchair and the fight to take her place at Stanford

Resveratrol found in grapes could help astronauts on Mars

New drug provides hope for patients with Duchenne muscular dystrophy

Researchers identify previously unknown autoimmune disease involving muscle pain, weakness

Lithium improves muscle size and strength in mice with limb girdle muscular dystrophy

Study demonstrates the concept of systemic gene therapy treatment for gamma-sarcoglycanopathy

Novo Biosciences achieves major milestones in its new drug to treat heart disease and DMD

Clinical study shows tolerability and safety of investigational drug in boys with DMD

UCL and AIIMS collaborates to increase academic and student exchange

Phase 1 data reinforce safety profile of new drug for treating Duchenne muscular dystrophy

Creative solutions to enhance patient's point of view in neuromuscular research

Neuroscience - Second Edition eBook

Achieving and maintaining ISO 27001 and BS 10012 certifications

Expanding research and clinical options for children with cancer

Examining how pain could play a direct protective role in the gut

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