Neuromuscular Disease News and Research

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ALS TDI forms research partnership with Neurimmune to advance potential treatments for ALS

ALS TDI forms research partnership with Neurimmune to advance potential treatments for ALS

Imaginative play with medically themed toys may improve recovery in chronically ill children

Imaginative play with medically themed toys may improve recovery in chronically ill children

Trophos completes efficacy study of olesoxime in patients with Spinal Muscular Atrophy

Trophos completes efficacy study of olesoxime in patients with Spinal Muscular Atrophy

Three Penn Medicine researchers awarded grants for neuromuscular disease research

Three Penn Medicine researchers awarded grants for neuromuscular disease research

Quintiles and MDA partner to develop U.S. Neuromuscular Disease Registry

Quintiles and MDA partner to develop U.S. Neuromuscular Disease Registry

Isis Pharmaceuticals announces preliminary data from ISIS-SMNRx Phase 1 study in infants with SMA

Isis Pharmaceuticals announces preliminary data from ISIS-SMNRx Phase 1 study in infants with SMA

Isis Pharmaceuticals starts ISIS-SMNRx Phase 2 study in infants with SMA

Isis Pharmaceuticals starts ISIS-SMNRx Phase 2 study in infants with SMA

DART Therapeutics develops new class of therapy for Duchenne muscular dystrophy

DART Therapeutics develops new class of therapy for Duchenne muscular dystrophy

Genetic testing services for rare neurological disorders launched by Athena Diagnostics

Genetic testing services for rare neurological disorders launched by Athena Diagnostics

Dementia diagnostic panel for treatable forms of cognitive impairment launched by Quest Diagnostics

Dementia diagnostic panel for treatable forms of cognitive impairment launched by Quest Diagnostics

Columbia University Medical Center, NewYork-Presbyterian Hospital present research works at AAN meeting

Columbia University Medical Center, NewYork-Presbyterian Hospital present research works at AAN meeting

Pivotal study of olesoxime in Spinal Muscular Atrophy receives positive interim review

Pivotal study of olesoxime in Spinal Muscular Atrophy receives positive interim review

Systemic delivery of antisense oligonucleotides neutralizes mutant RNA toxicity in mice with DM1

Systemic delivery of antisense oligonucleotides neutralizes mutant RNA toxicity in mice with DM1

CUMC receives $7M to help establish Weinberg Family Cerebral Palsy Center

CUMC receives $7M to help establish Weinberg Family Cerebral Palsy Center

Pfizer, Repligen sign licensing deal to advance spinal muscular atrophy program

Pfizer, Repligen sign licensing deal to advance spinal muscular atrophy program

Leg press power best indicator of function after knee arthroplasty

Leg press power best indicator of function after knee arthroplasty

‘Gene for speed’ researcher awarded Ramaciotti Medal

‘Gene for speed’ researcher awarded Ramaciotti Medal

Two CUMC studies provide new insights into spinal muscular atrophy

Two CUMC studies provide new insights into spinal muscular atrophy

Laminin-111 protein therapy could treat Duchenne muscular dystrophy

Laminin-111 protein therapy could treat Duchenne muscular dystrophy

UI Hospital implants NeuRx Diaphragm Pacing System in a patient with ALS

UI Hospital implants NeuRx Diaphragm Pacing System in a patient with ALS