Thalassemia News and Research

RSS
Thalassemia is a group of genetic blood disorders that affect approximately 1,000 individuals in the United States. The most severe of these disorders is Cooley's Anemia.

People with thalassemia have a genetic defect of their red blood cells that affects the cells' ability to produce normal hemoglobin. Red blood cells use hemoglobin to carry oxygen to tissues. As a result of the defect, most forms of thalassemia produce a chronic, lifelong anemia that begins in early childhood and often must be treated with frequent transfusions.
Better education and communication critical for increasing blood donation among minorities

Better education and communication critical for increasing blood donation among minorities

More screening and new treatments needed for sickle cell disease

More screening and new treatments needed for sickle cell disease

Scientists use gold nanoparticles to edit genes tied to HIV, inherited blood disorders

Scientists use gold nanoparticles to edit genes tied to HIV, inherited blood disorders

Study compares effectiveness and cost of gene therapy and HSCT in major beta-thalassemia

Study compares effectiveness and cost of gene therapy and HSCT in major beta-thalassemia

New gene therapy cures babies with fatal 'Bubble Boy' disease

New gene therapy cures babies with fatal 'Bubble Boy' disease

Researchers develop new strategy to treat sickle cell disease and beta thalassemia

Researchers develop new strategy to treat sickle cell disease and beta thalassemia

Study illuminates how hot spots of genetic variation evolved in the human genome

Study illuminates how hot spots of genetic variation evolved in the human genome

Deadly inherited blood disorders cured with bone marrow transplant

Deadly inherited blood disorders cured with bone marrow transplant

Antibody-based treatment could improve cure rate for blood and immune disorders

Antibody-based treatment could improve cure rate for blood and immune disorders

App that could detect level of anemia by looking at fingernails

App that could detect level of anemia by looking at fingernails

Advances in gene therapy for inherited blood disorders

Advances in gene therapy for inherited blood disorders

Bluebird bio collaborates with Gritstone Oncology to develop novel cancer cell therapies

Bluebird bio collaborates with Gritstone Oncology to develop novel cancer cell therapies

Regenacy Pharmaceuticals partners with CMTA to advance ricolinostat for treating hereditary neuropathy

Regenacy Pharmaceuticals partners with CMTA to advance ricolinostat for treating hereditary neuropathy

Therapy with L-Glutamine reduces pain in patients with sickle cell disease

Therapy with L-Glutamine reduces pain in patients with sickle cell disease

Researchers identify enzyme as potential new drug target for blood disorders

Researchers identify enzyme as potential new drug target for blood disorders

Mice study shows promise for treating genetic conditions during fetal development

Mice study shows promise for treating genetic conditions during fetal development

Research project offers hope for pediatric patients with thalassemia

Research project offers hope for pediatric patients with thalassemia

Celgene to share new and updated data around novel hematological therapies

Celgene to share new and updated data around novel hematological therapies

Study shows gene variations associated with malaria risk

Study shows gene variations associated with malaria risk

Smart Cells launches social campaign to support Rare Disease Day 2018

Smart Cells launches social campaign to support Rare Disease Day 2018