Pharmaceuticals News and Research

RSS

Alnylam’s patisiran receives positive opinion from CHMP for treating hATTR amyloidosis

Alnylam Pharmaceuticals, Inc., the leading RNAi therapeutics company, announced today that the Committee for Medicinal Products for Human Use has adopted a Positive Opinion recommending marketing authorization of patisiran for the treatment of hereditary transthyretin-mediated amyloidosis in adults with stage 1 or stage 2 polyneuropathy.

27 Jul 2018

Newer version of ALS drug may effectively treat inherited form of the disease

NIH-funded researchers delayed signs of amyotrophic lateral sclerosis in rodents by injecting them with a second-generation drug designed to silence the gene, superoxide dismutase 1.

27 Jul 2018

Bile acids from the gut may offer new treatment for cocaine abuse

Bile acids that aid fat digestion are also found to reduce the rewarding properties of cocaine use, according to a study publishing on July 26 in the open-access journal PLOS Biology by India Reddy, Nicholas Smith, and Robb Flynn of Vanderbilt University, Aurelio Galli of the University of Alabama at Birmingham, and colleagues.

27 Jul 2018

Surrey researchers design more efficient, flexible x-ray detector

Detectors that are presently used for mammograms and for dose measurements in radiotherapy are often rigid, causing errors in screening, or dose delivery to surrounding healthy tissue.

26 Jul 2018

Déjà voodoo: Pharma’s promises to curb drug prices have been heard before

Prescription drug prices were soaring. Angry policymakers swore they'd take action. Pharma giant Merck responded by promising to address the problem voluntarily, vowing to keep price increases under the overall rate of inflation.

25 Jul 2018

Pivotal study of dasotraline in adults with binge eating disorder meets primary endpoint

Sunovion Pharmaceuticals Inc. today announced that a study evaluating the efficacy and safety of dasotraline in adults with moderate to severe binge eating disorder met its primary endpoint, demonstrating a statistically significant decrease in number of binge days per week from baseline to Week 12 in the group treated with dasotraline 6 mg/day versus the placebo-treated group.

25 Jul 2018

New project explores health effects of dangerous chemicals

The EDC-MIXRISK project is exploring the health effects of a group of man-made substances that have been shown to disrupt the body’s endocrine system, the collection of hormone-producing glands that regulate growth and development, metabolism, reproduction and even mood and sleep patterns.

23 Jul 2018

FDA approves first drug for treatment of adult AML patients with specific genetic mutation

The U.S. Food and Drug Administration today approved Tibsovo (ivosidenib) tablets for the treatment of adult patients with relapsed or refractory acute myeloid leukemia (AML) who have a specific genetic mutation.

20 Jul 2018

AVITA Medical expands management team to support launch of RECELL device to treat burns

AVITA Medical today announced that it expanded its management team in the commercial, legal and medical affairs functions to support the planned U.S. launch of the RECELL® Autologous Cell Harvesting Device in the treatment of burns

20 Jul 2018

Ferring announces FDA approval of ZOMACTON for injection in four new pediatric indications

Ferring Pharmaceuticals Inc. today announced that the U.S. Food and Drug Administration has approved ZOMACTON for injection in four additional pediatric indications

20 Jul 2018

Top AI companies join hands to discover novel drugs for DMD

Insilico Medicine a leader in artificial intelligence for drug discovery, biomarker development and aging research, announced a research collaboration agreement with A2A Pharmaceuticals, Inc. A2A is a biotechnology company headquartered in New York and focused on development of novel drugs for unmet needs in oncology, drug resistant bacterial infections, and other life threatening diseases.

20 Jul 2018

Podcast: KHN’s ‘What the Health?’ Drug prices and unicorns

A trio of court actions provide news for this week's “What the Health?'” panel. A federal appeals court this week handed hospitals a setback in their effort to stop the Trump administration from cutting funding for a program that provides deep discounts on drugs.

19 Jul 2018

Research reveals long-term efficacy of drug used to treat common cause of kidney failure

New research provides support for the long-term efficacy of a drug used to treat in patients with autosomal dominant polycystic kidney disease, a common cause of kidney failure.

19 Jul 2018

Rat study shows negative effects of perinatal exposure to phthalates

Male and female rats exposed in the womb and during lactation to plasticizing chemicals known as phthalates had significantly fewer neurons and synapses than those that were not exposed, researchers report in a new study.

19 Jul 2018

FDA grants approval for first breast cancer drug through 'Real-Time Oncology Review'

The U.S. Food and Drug Administration today approved Kisqali (ribociclib) in combination with an aromatase inhibitor for the treatment of pre/perimenopausal or postmenopausal women with hormone receptor (HR)-positive, human epidermal growth factor receptor 2 (HER2)-negative advanced or metastatic breast cancer, as initial endocrine-based therapy.

19 Jul 2018

Staggering prices slow insurers’ coverage of CAR-T cancer therapy

Patients whose blood cancers have failed to respond to repeated rounds of chemotherapy may be candidates for a new type of gene therapy that could send their cancers into remission for years.

17 Jul 2018

'Skin Cancer, Take A Hike!' program promotes sun safety and skin cancer awareness

Skin cancer is the most common cancer in the United States, affecting one in five Americans in their lifetime.

13 Jul 2018

Podcast: KHN’s ‘What the Health?’ ACA under fire. Again.

Democrats in the Senate are gearing up to fight President Donald Trump's nominee to the Supreme Court, U.S. Circuit Judge Brett Kavanaugh. They argue he is not only a potential threat to abortion rights, but also to the Affordable Care Act.

13 Jul 2018

Aurinia’s Phase 2 trial evaluates voclosporin ophthalmic solution for treating dry eye syndrome

Aurinia Pharmaceuticals Inc., a clinical stage biopharmaceutical company focused on the global immunology market, today announced the initiation of its Phase 2 trial evaluating voclosporin ophthalmic solution (VOS) for the treatment of dry eye syndrome (DES).

12 Jul 2018

Researchers highlight the need for wider access to HIV prevention drugs

Despite highly effective anti-HIV pharmaceuticals having been used worldwide for almost a decade, HIV has not been conquered.

11 Jul 2018

Pharmaceuticals News and Research

Alnylam’s patisiran receives positive opinion from CHMP for treating hATTR amyloidosis

Newer version of ALS drug may effectively treat inherited form of the disease

Bile acids from the gut may offer new treatment for cocaine abuse

Surrey researchers design more efficient, flexible x-ray detector

Déjà voodoo: Pharma’s promises to curb drug prices have been heard before

Pivotal study of dasotraline in adults with binge eating disorder meets primary endpoint

New project explores health effects of dangerous chemicals

FDA approves first drug for treatment of adult AML patients with specific genetic mutation

AVITA Medical expands management team to support launch of RECELL device to treat burns

Ferring announces FDA approval of ZOMACTON for injection in four new pediatric indications

Top AI companies join hands to discover novel drugs for DMD

Podcast: KHN’s ‘What the Health?’ Drug prices and unicorns

Research reveals long-term efficacy of drug used to treat common cause of kidney failure

Rat study shows negative effects of perinatal exposure to phthalates

FDA grants approval for first breast cancer drug through 'Real-Time Oncology Review'

Staggering prices slow insurers’ coverage of CAR-T cancer therapy

'Skin Cancer, Take A Hike!' program promotes sun safety and skin cancer awareness

Podcast: KHN’s ‘What the Health?’ ACA under fire. Again.

Aurinia’s Phase 2 trial evaluates voclosporin ophthalmic solution for treating dry eye syndrome

Researchers highlight the need for wider access to HIV prevention drugs

Event guide: World ADC London eBook

Latest eBooks

Editorial Focus eBook - Spatial and single-cell omics (1st edition)

Industry Focus eBook - Analytical Chemistry (3rd edition)

Industry Focus eBook - Microbiome (1st edition)

Industry Focus eBook - Cell biology (5th edition)

Improving healthcare sustainability through carbon data

A New Approach to Preventing Bladder Cancer Recurrence

Bringing real-time analytics to downstream bioprocess monitoring