Severe Combined Immunodeficiency News and Research

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Researchers identify novel disorder resulting from a mutation in AIOLOS protein

Researchers identify novel disorder resulting from a mutation in AIOLOS protein

UCSF launches new initiative to propel the development of living therapeutics

UCSF launches new initiative to propel the development of living therapeutics

Investigational gene therapy can restore immune function in children with inherited immunodeficiency disorder

Investigational gene therapy can restore immune function in children with inherited immunodeficiency disorder

Experimental gene therapy successfully treats children born without an immune system

Experimental gene therapy successfully treats children born without an immune system

Scientists launch clinical trial of CRISPR gene correction therapy in patients with sickle cell disease

Scientists launch clinical trial of CRISPR gene correction therapy in patients with sickle cell disease

New test will help better manage patients with severe combined immunodeficiency

New test will help better manage patients with severe combined immunodeficiency

Research team generates comprehensive developmental map of human T-cells

Research team generates comprehensive developmental map of human T-cells

COVID-19 and immunodeficiency

COVID-19 and immunodeficiency

NIH grants boost rare diseases research efforts

NIH grants boost rare diseases research efforts

Despite failed promises, stem cell advocates again want taxpayers to pony up billions

Despite failed promises, stem cell advocates again want taxpayers to pony up billions

New gene therapy cures babies with fatal 'Bubble Boy' disease

New gene therapy cures babies with fatal 'Bubble Boy' disease

Antibody-based treatment could improve cure rate for blood and immune disorders

Antibody-based treatment could improve cure rate for blood and immune disorders

Leadiant Biosciences announces FDA approval of Revcovi for treating pediatric, adult ADA-SCID patients

Leadiant Biosciences announces FDA approval of Revcovi for treating pediatric, adult ADA-SCID patients

Using novel gene therapy to cure infants born with severe combined immunodeficiency

Using novel gene therapy to cure infants born with severe combined immunodeficiency

Smart Cells launches social campaign to support Rare Disease Day 2018

Smart Cells launches social campaign to support Rare Disease Day 2018

A guide to Severe Combined Immunodeficiency Disease, review released

A guide to Severe Combined Immunodeficiency Disease, review released

New review provides guidance to doctors who may treat infants with ‘bubble boy disease’

New review provides guidance to doctors who may treat infants with ‘bubble boy disease’

St. Jude gene therapy offers hope for infants with 'bubble boy' disease

St. Jude gene therapy offers hope for infants with 'bubble boy' disease

Orchard Therapeutics opens new facility for technical operations in San Francisco Bay area

Orchard Therapeutics opens new facility for technical operations in San Francisco Bay area

Study to determine lowest dose of chemotherapy needed for babies with SCID

Study to determine lowest dose of chemotherapy needed for babies with SCID