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Study examines clinical risk factors for kidney function decline in children with CKD

Study examines clinical risk factors for kidney function decline in children with CKD

Cryo-EM reveals the structure of hnRNPDL-2 protein fibrils associated with limb-girdle muscular dystrophy

Cryo-EM reveals the structure of hnRNPDL-2 protein fibrils associated with limb-girdle muscular dystrophy

Researchers develop a cell line to address the challenges facing cellular modeling of disease

Researchers develop a cell line to address the challenges facing cellular modeling of disease

New 'cutting edge' hemophilia treatment is a victory for patients, Tulane doctor says

New 'cutting edge' hemophilia treatment is a victory for patients, Tulane doctor says

Using motion capture technology and AI to monitor the progression of movement disorders

Using motion capture technology and AI to monitor the progression of movement disorders

UK set to boost genomics expertise through a landmark partnership with Thailand

UK set to boost genomics expertise through a landmark partnership with Thailand

What does the future of clinical trials and evidence-based medicine look like?

What does the future of clinical trials and evidence-based medicine look like?

Researchers develop innovative STAb therapy for a type of leukemia

Researchers develop innovative STAb therapy for a type of leukemia

Incurable liver disease could be reversed with a single drug

Incurable liver disease could be reversed with a single drug

Study shows the clinical utility of amniotic fluid cells RNA-sequencing in prenatal rare disease diagnosis

Study shows the clinical utility of amniotic fluid cells RNA-sequencing in prenatal rare disease diagnosis

NCI-led clinical trial results in the first approval of a treatment for advanced alveolar soft part sarcoma

NCI-led clinical trial results in the first approval of a treatment for advanced alveolar soft part sarcoma

Study shows positive effect of concentrating surgery for children with neuroblastoma

Study shows positive effect of concentrating surgery for children with neuroblastoma

Two Cents' Worth: Shared decision making in renal cell carcinoma (RCC)

Two Cents' Worth: Shared decision making in renal cell carcinoma (RCC)

Updated guidelines seek to improve transparency and utility in clinical trial reporting

Updated guidelines seek to improve transparency and utility in clinical trial reporting

CRISPR/Cas9-engineered avatar mouse model of rare disease paves the way for targeted therapy

CRISPR/Cas9-engineered avatar mouse model of rare disease paves the way for targeted therapy

GOSH delivers world-first base-edited cell therapy for a patient with relapsed T cell leukemia

GOSH delivers world-first base-edited cell therapy for a patient with relapsed T cell leukemia

Research extends the powerful tool of immunotherapy to autoimmune diseases

Research extends the powerful tool of immunotherapy to autoimmune diseases

New tool may help better predict resistance to immunoglobulin therapy among children with Kawasaki disease

New tool may help better predict resistance to immunoglobulin therapy among children with Kawasaki disease

Cannabidiol and the shifting perspective of epilepsy drug discovery

Cannabidiol and the shifting perspective of epilepsy drug discovery

UAB and Menkes International Association sign a donation agreement to boost research in Menkes disease

UAB and Menkes International Association sign a donation agreement to boost research in Menkes disease